HELIOS-A: IMPACT OF VUTRISIRAN ON QUALITY OF LIFE AND FUNCTIONAL STATUS IN HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS

被引：0

作者：

Ajroud-Driss, Senda ^{[1
]}

Berk, John L. ^{[2
]}

Adams, David ^{[3
,4
]}

Gillmore, Julian ^{[5
]}

Lin, Kon-Ping ^{[6
]}

Kale, Parag ^{[7
]}

Koike, Haruki ^{[8
]}

Aldinc, Emre ^{[9
]}

Chen, Chongshu ^{[9
]}

Vest, John ^{[9
]}

Obici, Laura ^{[10
]}

机构：

[1] Northwestern Univ, Feinberg Sch Med, Dept Med Social Sci, Neurol, Chicago, IL 60611 USA

[2] Boston Med Ctr, Boston, MA USA

[3] Univ Paris Saclay, INSERM, U1195, Le Kremlin Bicetre, France

[4] CHU Bicetre, AP HP, Neurol Dept, Le Kremlin Bicetre, France

[5] UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England

[6] Taipei Vet Gen Hosp, Dept Neurol, Taipei, Taiwan

[7] Baylor Univ, Med Ctr, Dallas, TX USA

[8] Nagoya Univ, Dept Neurol, Grad Sch Med, Nagoya, Aichi, Japan

[9] Alnylam Pharmaceut, Cambridge, MA USA

[10] IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy

来源：

JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2023年 / 28卷

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：S40 / S41

页数：2

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