Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors (vol 18, pg 2099, 2009)

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HUMAN MOLECULAR GENETICS | 2023年 / 32卷 / 24期
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D O I：
10.1093/hmg/ddad169
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Q5 [生物化学]; Q7 [分子生物学];
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071010 ; 081704 ;
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页码：3391 / 3393
页数：3
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  • [1] Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors (vol 18, pg 2099, 2009)
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