共 39 条
- [1] Multiplexed comparison of rationally-designed AAV CNS capsids in vivoHUMAN GENE THERAPY, 2024, 35 (3-4) : A107 - A107Yebra-Pimentel, E. Santidrian论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsKieper, S.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, Netherlandsvan der Zon, T.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsMomchev, L.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsMoreno, F.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsBosma, B.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsBashir, N.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsWaaijer, S.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsHoornenborg, W.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsHeidinga, N.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsHoogland, T.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsPesic, M.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, NetherlandsKusuma, A.论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharma BV, Amsterdam, Netherlands UniQure Biopharma BV, Amsterdam, Netherlands
- [2] Rationally Engineered AAV Capsids Improve Transduction and Volumetric Spread in the CNSMOLECULAR THERAPY-NUCLEIC ACIDS, 2017, 8 : 184 - 197Kanaan, Nicholas M.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USA Mercy Hlth St Marys, Grand Rapids, MI 49503 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USASellnow, Rhyomi C.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USABoye, Sanford L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Gainesville, FL 32610 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USACoberly, Ben论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USA Michigan State Univ, Neurosci Program, E Lansing, MI 48825 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USABennett, Antonette论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USAAgbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Dept Biochem & Mol Biol, McKnight Brain Inst, Gainesville, FL 32610 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USASortwell, Caryl E.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USA Mercy Hlth St Marys, Grand Rapids, MI 49503 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USAHauswirth, William W.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Gainesville, FL 32610 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USABoye, Shannon E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Gainesville, FL 32610 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USAManfredsson, Fredric P.论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USA Mercy Hlth St Marys, Grand Rapids, MI 49503 USA Michigan State Univ, Dept Translat Sci & Mol Med, 333 Bostwick Ave NE, Grand Rapids, MI 49503 USA
- [3] Rationally Engineered Novel AAV Capsids for Intraarticular Gene DeliveryMOLECULAR THERAPY, 2023, 31 (04) : 651 - 652Li, Wenjun论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC USA Univ N Carolina, Chapel Hill, NC USASamulski, R. Jude论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC USA Univ N Carolina, Chapel Hill, NC USALi, Chengwen论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC USA Univ N Carolina, Chapel Hill, NC USA
- [4] Rationally engineered novel AAV capsids for intra-articular gene deliveryMOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT, 2024, 32 (01)Li, Wenjun论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ N Carolina, Div Oral & Craniofacial Biomed, Adams Sch Dent, Chapel Hill, NC USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USAFeng, Susi Liu论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USAHerrschaft, Lizette论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USASamulski, R. Jude论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Dept Pharmacol, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USALi, Chengwen论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Dept Pediat, Chapel Hill, NC 27599 USA Univ North Carolina Chapel Hill, Carolina Inst Dev Disabil, Chapel Hill, NC 27510 USA Univ North Carolina Chapel Hill, Gene Therapy Ctr, Chapel Hill, NC 27599 USA
- [5] Directed Evolution of Rationally-Engineered AAV Capsid Variants with Enhanced Central Nervous System (CNS) Tropism Following Systematic AdministrationMOLECULAR THERAPY, 2024, 32 (04) : 480 - 480Wang, Hongxing论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut, Lexington, MA USA NeuShen Therapeut, Lexington, MA USAZhu, Sha论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut, Lexington, MA USA NeuShen Therapeut, Lexington, MA USAZhang, Weiqun论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut, Lexington, MA USA NeuShen Therapeut, Lexington, MA USAToro, Gabriela C.论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut, Lexington, MA USA NeuShen Therapeut, Lexington, MA USALiu, Na论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut, Lexington, MA USA NeuShen Therapeut, Lexington, MA USAZhao, Lingzhi论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut, Lexington, MA USA NeuShen Therapeut, Lexington, MA USAShen, Joan论文数: 0 引用数: 0 h-index: 0机构: NeuShen Therapeut, Lexington, MA USA NeuShen Therapeut, Lexington, MA USA
- [6] In Vivo targeting of HSC by capsid-engineered AAV vectorsHUMAN GENE THERAPY, 2024, 35 (3-4) : A9 - A10Meumann, N.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, GermanyRadtke, S.论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Ctr, Seattle, WA USA Hannover Med Sch, Hannover, GermanyGarmendia, X. Perez论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, GermanyJust, S.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, GermanyGutierrez, A. Fornell论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, GermanyErtelt, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Leipzig, Fac Med, Leipzig, Germany Hannover Med Sch, Hannover, GermanySchoeder, C. T.论文数: 0 引用数: 0 h-index: 0机构: Univ Leipzig, Fac Med, Leipzig, Germany Hannover Med Sch, Hannover, GermanyKuhlmann, A. S.论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Ctr, Seattle, WA USA Hannover Med Sch, Hannover, GermanyPeterson, C. W.论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Ctr, Seattle, WA USA Hannover Med Sch, Hannover, GermanyStone, D.论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Ctr, Seattle, WA USA Hannover Med Sch, Hannover, GermanyJerome, K.论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Ctr, Seattle, WA USA Hannover Med Sch, Hannover, GermanyKiem, H. P.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, GermanyBuening, H.论文数: 0 引用数: 0 h-index: 0机构: Hannover Med Sch, Hannover, Germany Hannover Med Sch, Hannover, Germany
- [7] Process and Platform Development for Production and Purification of CNS-Tropic Engineered AAV CapsidsMOLECULAR THERAPY, 2023, 31 (04) : 688 - 689Xie, Zelong论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAKim, Taeho论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAOjala, David论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Richmond, CA USA Sangamo Therapeut Inc, Brisbane, CA USAPadilla, Jada论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAYadav, Sandeep论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USAChikere, Anthony论文数: 0 引用数: 0 h-index: 0机构: Sangamo Therapeut Inc, Brisbane, CA USA Sangamo Therapeut Inc, Brisbane, CA USA
- [8] Engineered AAV capsid transport mutants overcome transduction deficiencies in the aged CNSMOLECULAR THERAPY NUCLEIC ACIDS, 2024, 35 (04):Sandoval, Ivette M.论文数: 0 引用数: 0 h-index: 0机构: Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USAKelley, Christy M.论文数: 0 引用数: 0 h-index: 0机构: Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USABernal-Conde, Luis Daniel论文数: 0 引用数: 0 h-index: 0机构: Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USASteece-Collier, Kathy论文数: 0 引用数: 0 h-index: 0机构: Michigan State Univ, Coll Human Med, Dept Translat Neurosci, Grand Rapids, MI 49503 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USAMarmion, David J.论文数: 0 引用数: 0 h-index: 0机构: Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USA论文数: 引用数: h-index:机构:Crosson, Sean M.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Div Cellular & Mol Therapy, Gainesville, FL 32610 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USABoye, Sanford L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Powell Gene Therapy Ctr, Dept Pediat, Gainesville, FL 32610 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USABoye, Shannon E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Div Cellular & Mol Therapy, Gainesville, FL 32610 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USAManfredsson, Fredric P.论文数: 0 引用数: 0 h-index: 0机构: Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USA Barrow Neurol Inst, Dept Translat Neurosci, Parkinsons Dis Res Unit, Phoenix, AZ 85013 USA
- [9] A Rationally Engineered Capsid Variant of AAV9 for Systemic CNS-Directed and Peripheral Tissue-Detargeted Gene Delivery in NeonatesMOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2018, 9 : 234 - 246Wang, Dan论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USALi, Shaoyong论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAGessler, Dominic J.论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAXie, Jun论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAZhong, Li论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USALi, Jia论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USATran, Karen论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAVan Vliet, Kim论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USARen, Lingzhi论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Viral Vector Core, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAHe, Ran论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Viral Vector Core, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAGoetzmann, Jason E.论文数: 0 引用数: 0 h-index: 0机构: Univ Louisiana Lafayette, New Iberia Res Ctr, New Iberia, LA 70560 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAFlotte, Terence R.论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Dept Pediat, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAAgbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA Univ Massachusetts, Li Weibo Inst Rare Dis Res, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Dept Microbiol & Physiol Syst, Sch Med, Worcester, MA 01605 USA Univ Massachusetts, Viral Vector Core, Sch Med, Worcester, MA 01605 USA Sichuan Univ, West China Hosp, Chengdu 610041, Sichuan, Peoples R China Univ Massachusetts, Horae Gene Therapy Ctr, Sch Med, 368 Plantat St,AS6-2049, Worcester, MA 01605 USA
- [10] A Rationally Engineered Novel Capsid Variant of AAV9 for Pripheral Tissue-Detargeted and CNS-Directed Systemic Gene DeliveryMOLECULAR THERAPY, 2013, 21 : S2 - S2Zhong, Li论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Pediat, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Shaoyong论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Microbio & Physiol Syst, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAVliet, Kim Van论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Mengxin论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAXie, Jun论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Jia论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAHe, Ran论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAZhang, Yu论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USALi, Huapeng论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAWang, Dan论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAGoetzmann, Jason论文数: 0 引用数: 0 h-index: 0机构: Univ Louisiana Lafayette, New Iberia Res Ctr, New Iberia, LA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAFlotte, Terence R.论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Pediat, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAAgbandje-McKenna, Mavis论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Biochem & Mol Biol, Gainesville, FL 32610 USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA UMass Med Sch, Dept Microbio & Physiol Syst, Worcester, MA USA UMass Med Sch, Gene Therapy Ctr, Worcester, MA USA