Gene Therapy Using a CNS Dominant Human FMRP Isoform Rescues Seizures, Fear Conditioning, and Sleep Abnormalities in Fmr1 KO Mice

被引：0

|

作者：

Wong, Hayes ^{[1
]}

Hooper, Alex ^{[1
]}

Kang, Hye Ri ^{[2
]}

Lee, Shiron J. ^{[1
]}

Zhao, Jiayi ^{[1
]}

Sadhu, Chanchal ^{[3
]}

Rawat, Satinder ^{[3
]}

Gray, Steven J. ^{[2
]}

Hampson, David R. ^{[1
]}

机构：

[1] Univ Toronto, Leslie Dan Fac Pharm, Toronto, ON, Canada

[2] Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA

[3] Taysha Gene Therapies Inc, Dallas, TX USA

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

679

引用

收藏

页码：339 / 339

页数：1

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