In Vivo Gene Therapy for Lysosomal Acid Lipase Deficiency

被引：0

作者：

Laurent, Marine ^{[1
]}

Jenny, Christine ^{[1
]}

Oustelandt, Julie ^{[1
]}

Brassier, Anais ^{[2
]}

Landini, Francesca ^{[3
]}

Pacelli, Consiglia ^{[3
]}

Ronzitti, Giuseppe ^{[1
,3
]}

Amendola, Mario ^{[1
,3
]}

机构：

[1] Genethon, UMRS 951, Evry, France

[2] Necker Enfants Malades Univ Hosp, Paris, France

[3] Univ Foggia, Dept Clin & Expt Med, Foggia, Italy

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

643

引用

页码：322 / 323

页数：2

共 50 条

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