In Vivo Gene Therapy for Lysosomal Acid Lipase Deficiency

被引：0
作者：
Laurent, Marine [1 ]
Jenny, Christine [1 ]
Oustelandt, Julie [1 ]
Brassier, Anais [2 ]
Landini, Francesca [3 ]
Pacelli, Consiglia [3 ]
Ronzitti, Giuseppe [1 ,3 ]
Amendola, Mario [1 ,3 ]
机构：
[1] Genethon, UMRS 951, Evry, France
[2] Necker Enfants Malades Univ Hosp, Paris, France
[3] Univ Foggia, Dept Clin & Expt Med, Foggia, Italy
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
643
引用
收藏
页码：322 / 323
页数：2
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