共 42 条
- [11] Revisiting the "New'' Inflammatory Toxicities of Adeno-Associated Virus Vectors[J]. Flotte, Terence R. HUMAN GENE THERAPY, 2020(7-8)
- [12] The Effects of LY2405319, an FGF21 Analog, in Obese Human Subjects with Type 2 Diabetes[J]. Gaich, Gregory;Chien, Jenny Y.;Fu, Haoda;Glass, Leonard C.;Deeg, Mark A.;Holland, William L.;Kharitonenkov, Alexei;Bumol, Thomas;Schilske, Holger K.;Moller, David E. CELL METABOLISM, 2013(03)
- [13] AAV-expressed eCD4-Ig provides durable protection from multiple SHIV challenges[J]. Gardner, Matthew R.;Kattenhorn, Lisa M.;Kondur, Hema R.;von Schaewen, Markus;Dorfman, Tatyana;Chiang, Jessica J.;Haworth, Kevin G.;Decker, Julie M.;Alpert, Michael D.;Bailey, Charles C.;Neale, Ernest S., Jr.;Fellinger, Christoph H.;Joshi, Vinita R.;Fuchs, Sebastian P.;Martinez-Navio, Jose M.;Quinlan, Brian D.;Yao, Annie Y.;Mouquet, Hugo;Gorman, Jason;Zhang, Baoshan;Poignard, Pascal;Nussenzweig, Michel C.;Burton, Dennis R.;Kwong, Peter D.;Piatak, Michael, Jr.;Lifson, Jeffrey D.;Gao, Guangping;Desrosiers, Ronald C.;Evans, David T.;Hahn, Beatrice H.;Ploss, Alexander;Cannon, Paula M.;Seaman, Michael S.;Farzan, Michael. NATURE, 2015(7541)
- [14] Rationale-Based Engineering of a Potent Long-Acting FGF21 Analog for the Treatment of Type 2 Diabetes[J]. Hecht, Randy;Li, Yue-Sheng;Sun, Jeonghoon;Belouski, Ed;Hall, Michael;Hager, Todd;Yie, Junming;Wang, Wei;Winters, Dwight;Smith, Stephen;Spahr, Chris;Tam, Lei-Ting;Shen, Zhongnan;Stanislaus, Shanaka;Chinookoswong, Narumol;Lau, Yvonne;Sickmier, Allen;Michaels, Mark Leo;Boone, Thomas;Veniant, Murielle M.;Xu, Jing. PLOS ONE, 2012(11)
- [15] FGF21 gene therapy as treatment for obesity and insulin resistance[J]. Jimenez, Veronica;Jambrina, Claudia;Casana, Estefania;Sacristan, Victor;Munoz, Sergio;Darriba, Sara;Rodo, Jordi;Mallol, Cristina;Garcia, Miquel;Leon, Xavier;Marco, Sara;Ribera, Albert;Elias, Ivet;Casellas, Alba;Grass, Ignasi;Elias, Gemma;Ferre, Tura;Motas, Sandra;Franckhauser, Sylvie;Mulero, Francisca;Navarro, Marc;Haurigot, Virginia;Ruberte, Jesus;Bosch, Fatima. EMBO MOLECULAR MEDICINE, 2018(08)
- [16] Recombinant Adeno-Associated Viral Vectors Expressing Human Coagulation FIX-E456H Variant in Hemophilia B Mice[J]. Le Quellec, Sandra;Dane, Allison P.;Barbon, Elena;Bordet, Jean-Claude;Mingozzi, Federico;Dargaud, Yesim;Marais, Thibaut;Biferi, Maria-Grazia;Negrier, Claude;Nathawani, Amit C.;Enjolras, Nathalie. THROMBOSIS AND HAEMOSTASIS, 2019(12)
- [17] Potential limits of AAV-based gene therapy with the use of new transgenes expressing factor IX fusion proteins[J]. Le Quellec, Sandra;Dane, Allison;Enjolras, Nathalie;McIntosh, Jenny;Rosales, Cecilia;Negrier, Claude;Nathwani, Amit. HAEMOPHILIA, 2019(01)
- [18] Engineering adeno-associated virus vectors for gene therapy[J]. Li, Chengwen;Samulski, R. Jude. NATURE REVIEWS GENETICS, 2020(04)
- [19] Broad and potent bispecific neutralizing antibody gene delivery using adeno-associated viral vectors for passive immunization against HIV-1[J]. Li, Shuang;Qiao, Yongbo;Jiang, Shun;Wang, Bo;Kong, Wei;Shan, Yaming. JOURNAL OF CONTROLLED RELEASE, 2021
- [20] Dual inhibiting OCT4 and AKT potently suppresses the propagation of human cancer cells[J]. Li, Wenxin;Zhou, Yanwen;Zhang, Xiaoqian;Yang, Ying;Dan, Songsong;Su, Tong;She, Shiqi;Dong, Weilai;Zhao, Qingwei;Jia, Jia;Yao, Hangping;Zheng, Min;Kang, Bo;Wang, Ying-Jie. SCIENTIFIC REPORTS, 2017