Editorial: Genome editing applications of CRISPR/Cas9 in metabolic diseases, hormonal system and cancer research

被引:5
作者
Liu, Pengpeng [1 ]
Huang, Lei [1 ]
Song, Chun-Qing [2 ]
机构
[1] Univ Massachusetts, Mol Cell & Canc Biol MCCB, Med Sch, Worcester, MA 01605 USA
[2] Westlake Inst Adv Study, Inst Basic Med Sci, Hangzhou, Zhejiang, Peoples R China
关键词
CRISPR/Cas9; genome editing; metabolic diseases; hormonal system disease; cancer research;
D O I
10.3389/fendo.2023.1256966
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页数:2
相关论文
共 10 条
[1]  
Cameron P, 2017, NAT METHODS, V14, P600, DOI [10.1038/NMETH.4284, 10.1038/nmeth.4284]
[2]   Cas9-crRNA ribonucleoprotein complex mediates specific DNA cleavage for adaptive immunity in bacteria [J].
Gasiunas, Giedrius ;
Barrangou, Rodolphe ;
Horvath, Philippe ;
Siksnys, Virginijus .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2012, 109 (39) :E2579-E2586
[3]   Cas9 specifies functional viral targets during CRISPR-Cas adaptation [J].
Heler, Robert ;
Samai, Poulami ;
Modell, Joshua W. ;
Weiner, Catherine ;
Goldberg, Gregory W. ;
Bikard, David ;
Marraffini, Luciano A. .
NATURE, 2015, 519 (7542) :199-+
[4]   Somatic genome editing with CRISPR/Cas9 generates and corrects a metabolic disease [J].
Jarrett, Kelsey E. ;
Lee, Ciaran M. ;
Yeh, Yi-Hsien ;
Hsu, Rachel H. ;
Gupta, Rajat ;
Zhang, Min ;
Rodriguez, Perla J. ;
Lee, Chang Seok ;
Gillard, Baiba K. ;
Bissig, Karl-Dimiter ;
Pownall, Henry J. ;
Martin, James F. ;
Bao, Gang ;
Lagor, William R. .
SCIENTIFIC REPORTS, 2017, 7
[5]   Loss-of-function of IFT88 determines metabolic phenotypes in thyroid cancer [J].
Lee, Junguee ;
Yi, Shinae ;
Won, Minho ;
Song, Young Shin ;
Yi, Hyon-Seung ;
Park, Young Joo ;
Park, Ki Cheol ;
Kim, Jung Tae ;
Chang, Joon Young ;
Lee, Min Joung ;
Sul, Hae Joung ;
Choi, Ji Eun ;
Kim, Koon Soon ;
Kero, Jukka ;
Kim, Joon ;
Shong, Minho .
ONCOGENE, 2018, 37 (32) :4455-4474
[6]   Genome editing in primary cells and in vivo using viral-derived Nanoblades loaded with Cas9-sgRNA ribonucleoproteins [J].
Mangeot, Philippe E. ;
Risson, Valerie ;
Fusil, Floriane ;
Marnef, Aline ;
Laurent, Emilie ;
Blin, Juliana ;
Mournetas, Virginie ;
Massourides, Emmanuelle ;
Sohier, Thibault J. M. ;
Corbin, Antoine ;
Aube, Fabien ;
Teixeira, Marie ;
Pinset, Christian ;
Schaeffer, Laurent ;
Legube, Gaelle ;
Cosset, Francois-Loic ;
Verhoeyen, Els ;
Ohlmann, Theophile ;
Ricci, Emiliano P. .
NATURE COMMUNICATIONS, 2019, 10 (1)
[7]   DNA interrogation by the CRISPR RNA-guided endonuclease Cas9 [J].
Sternberg, Samuel H. ;
Redding, Sy ;
Jinek, Martin ;
Greene, Eric C. ;
Doudna, Jennifer A. .
NATURE, 2014, 507 (7490) :62-+
[8]   Highly efficient therapeutic gene editing of human hematopoietic stem cells [J].
Wu, Yuxuan ;
Zeng, Jing ;
Roscoe, Benjamin P. ;
Liu, Pengpeng ;
Yao, Qiuming ;
Lazzarotto, Cicera R. ;
Clement, Kendell ;
Cole, Mitchel A. ;
Luk, Kevin ;
Baricordi, Cristina ;
Shen, Anne H. ;
Ren, Chunyan ;
Esrick, Erica B. ;
Manis, John P. ;
Dorfman, David M. ;
Williams, David A. ;
Biffi, Alessandra ;
Brugnara, Carlo ;
Biasco, Luca ;
Brendel, Christian ;
Pinello, Luca ;
Tsai, Shengdar Q. ;
Wolfe, Scot A. ;
Bauer, Daniel E. .
NATURE MEDICINE, 2019, 25 (05) :776-+
[9]   CRISPR/Cas9-3NLS/sgHMGA2@PDA nanosystem is the potential efficient gene editing therapy for gastric cancer with HMGA2 high expression [J].
Wu, Zhouying ;
Huo, Xue ;
Yang, Tingyu ;
Liu, Kun ;
Wu, Ting ;
Feng, Zongqi ;
Wang, Min ;
Li, Feng ;
Jia, Jianchao ;
Zhang, Xiaoran ;
Gao, Wenming ;
Yu, Lan .
FRONTIERS IN ONCOLOGY, 2022, 12
[10]   Application of the CRISPR/Cas9-based gene editing technique in basic research, diagnosis, and therapy of cancer [J].
Zhang, Huimin ;
Qin, Chunhong ;
An, Changming ;
Zheng, Xiwang ;
Wen, Shuxin ;
Chen, Wenjie ;
Liu, Xianfang ;
Lv, Zhenghua ;
Yang, Pingchang ;
Xu, Wei ;
Gao, Wei ;
Wu, Yongyan .
MOLECULAR CANCER, 2021, 20 (01)