Hematopoietic Stem Cell Gene Therapy for Mucopolysaccharidosis Type IIIC

被引：0

作者：

Badell-Grau, Rafael A. ^{[1
]}

Sivakumar, Anusha ^{[1
]}

Khare, Veenita ^{[2
]}

Duong, Kalvin ^{[1
]}

Losay, Pauline ^{[1
]}

Pakravesh, Kasra ^{[1
]}

Tran, Christine ^{[1
]}

Pithia, Rushil ^{[1
]}

Lengsfield, Mira ^{[1
]}

Thai, Kevin ^{[1
]}

Sharma, Jay ^{[1
]}

Chen, Rola ^{[1
]}

Rainaldi, Joseph N. ^{[1
]}

Cherqui, Stephanie ^{[1
]}

机构：

[1] Univ Calif San Diego, La Jolla, CA USA

[2] Univ Calif San Diego, San Diego, CA USA

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

649

引用

页码：325 / 326

页数：2

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