Spinal muscular atrophy (SMA) is a genetic disorder which is clinically characterized by progressive muscle weakness and atrophy and is associated with the degeneration of spinal and lowers bulbar mot
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Ottawa Hosp, Res Inst, Regenerat Med Program, Ottawa, ON K1H 8L6, Canada
Univ Ottawa, Fac Med, Dept Biochem Microbiol & Immunol, Ottawa, ON, CanadaOttawa Hosp, Res Inst, Regenerat Med Program, Ottawa, ON K1H 8L6, Canada
Goulet, B. B.
Kothary, R.
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Ottawa Hosp, Res Inst, Regenerat Med Program, Ottawa, ON K1H 8L6, Canada
Univ Ottawa, Fac Med, Dept Cellular & Mol Med, Ottawa, ON, CanadaOttawa Hosp, Res Inst, Regenerat Med Program, Ottawa, ON K1H 8L6, Canada
Kothary, R.
Parks, R. J.
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Ottawa Hosp, Res Inst, Regenerat Med Program, Ottawa, ON K1H 8L6, Canada
Univ Ottawa, Fac Med, Dept Biochem Microbiol & Immunol, Ottawa, ON, Canada
Univ Ottawa, Dept Med, Fac Med, Ottawa, ON, CanadaOttawa Hosp, Res Inst, Regenerat Med Program, Ottawa, ON K1H 8L6, Canada
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Univ Michigan, Sch Med, Dept Pathol, Ann Arbor, MI USAThomas Jefferson Univ, Sidney Kimmel Med Coll, Dept Biochem & Mol Biol, Jefferson Alumni Hall,Rm 411E, Philadelphia, PA 19107 USA
Lieberman, Andrew P.
Merry, Diane E.
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Thomas Jefferson Univ, Sidney Kimmel Med Coll, Dept Biochem & Mol Biol, Jefferson Alumni Hall,Rm 411E, Philadelphia, PA 19107 USAThomas Jefferson Univ, Sidney Kimmel Med Coll, Dept Biochem & Mol Biol, Jefferson Alumni Hall,Rm 411E, Philadelphia, PA 19107 USA