Efficacy and Safety of BRL-101, CRISPR-Cas9-mediated Gene Editing of The BCL11A Enhancer in Transfusion-dependent β-thalassemia and Severe Sickle Cell Disease

被引：0

作者：

Zheng, Biao

Liu, Rongrong ^{[1
]}

Zhang, Xinhua ^{[2
]}

Bin Fu ^{[3
]}

Xu, Yajing ^{[3
]}

Shi, Jun ^{[4
]}

Feng, Xiaoqin ^{[5
]}

Wang, Chris ^{[6
]}

Li, Dali ^{[6
]}

Wu, Yuxuan ^{[6
]}

Liu, Mingyao ^{[6
]}

Lai, Yongrong ^{[1
]}

机构：

[1] Guangxi Med Univ, Affiliated Hosp 1, Nanning, Peoples R China

[2] 923Rd Hosp PLA, Shanghai, Peoples R China

[3] Cent South Univ, Xiangya Hosp, Changsha, Hunan, Peoples R China

[4] Chinese Acad Med Sci, Inst Hematol & Blood Dis Hosp, Tianjin, Peoples R China

[5] Southern Med Univ, Nanfang Hosp, Guangzhou, Peoples R China

[6] BRL Med Inc, Shanghai, Peoples R China

来源：

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

1858

引用

页数：2