Disease-Modifying Therapies in Parkinson's Disease

被引:0
作者
Fabbri, Margherita [1 ]
Corvol, Jean Christophe [2 ]
Rascol, Olivier [1 ]
机构
[1] Univ Toulouse, CHU Toulouse, Toulouse NeuroToul Ctr Excellence Neurodegenerat C, Dept Clin Pharmacol & Neurosci,INSERM,Clin Invest, Toulouse, France
[2] Sorbonne Univ, Assistance Publ Hop Paris, Hop Pitie Salpetriere, Paris Brain Inst ICM,INSERM,CNRS,French NS Pk F CR, Paris, France
关键词
Disease modifying; Parkinson's disease; Clinical trials; Biomarkers; Outcomes; Platform trials; ALPHA-SYNUCLEIN; DOUBLE-BLIND; CLINICAL-TRIAL; PROGRESSION; SAFETY; TOLERABILITY; MULTICENTER; DEFICIENCY; LEVODOPA; EFFICACY;
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
引用
收藏
页码:319 / 340
页数:22
相关论文
共 87 条
[1]   Glucocerebrosidase activity in Parkinson's disease with and without GBA mutations [J].
Alcalay, Roy N. ;
Levy, Oren A. ;
Waters, Cheryl C. ;
Fahn, Stanley ;
Ford, Blair ;
Kuo, Sheng-Han ;
Mazzoni, Pietro ;
Pauciulo, Michael W. ;
Nichols, William C. ;
Gan-Or, Ziv ;
Rouleau, Guy A. ;
Chung, Wendy K. ;
Wolf, Pavlina ;
Oliva, Petra ;
Keutzer, Joan ;
Marder, Karen ;
Zhang, Xiaokui .
BRAIN, 2015, 138 :2648-2658
[2]   The Impact of Type 2 Diabetes in Parkinson's Disease [J].
Athauda, Dilan ;
Evans, James ;
Wernick, Anna ;
Virdi, Gurvir ;
Choi, Minee L. ;
Lawton, Michael ;
Vijiaratnam, Nirosen ;
Girges, Christine ;
Ben-Shlomo, Yoav ;
Ismail, Khalida ;
Morris, Huw ;
Grosset, Donald ;
Foltynie, Thomas ;
Gandhi, Sonia .
MOVEMENT DISORDERS, 2022, 37 (08) :1612-1623
[3]   Exenatide once weekly versus placebo in Parkinson's disease: a randomised, double-blind, placebo-controlled trial [J].
Athauda, Dilan ;
Maclagan, Kate ;
Skene, Simon S. ;
Bajwa-Joseph, Martha ;
Letchford, Dawn ;
Chowdhury, Kashfia ;
Hibbert, Steve ;
Budnik, Natalia ;
Zampedri, Luca ;
Dickson, John ;
Li, Yazhou ;
Aviles-Olmos, Iciar ;
Warner, Thomas T. ;
Limousin, Patricia ;
Lees, Andrew J. ;
Greig, Nigel H. ;
Tebbs, Susan ;
Foltynie, Thomas .
LANCET, 2017, 390 (10103) :1664-1675
[4]   Impaired brain insulin signalling in Parkinson's disease [J].
Bassil, Fares ;
Delamarre, Anna ;
Canron, Marie-Helene ;
Dutheil, Nathalie ;
Vital, Anne ;
Negrier-Leibreich, Marie-Laure ;
Bezard, Erwan ;
Fernagut, Pierre-Olivier ;
Meissner, Wassilios G. .
NEUROPATHOLOGY AND APPLIED NEUROBIOLOGY, 2022, 48 (01)
[5]   A Randomized Clinical Trial of High-Dosage Coenzyme Q10 in Early Parkinson Disease No Evidence of Benefit [J].
Beal, M. Flint ;
Oakes, David ;
Shoulson, Ira ;
Henchcliffe, Claire ;
Galpern, Wendy R. ;
Haas, Richard ;
Juncos, Jorge L. ;
Nutt, John G. ;
Voss, Tiffini Smith ;
Ravina, Bernard ;
Shults, Clifford M. ;
Helles, Karen ;
Snively, Victoria ;
Lew, Mark F. ;
Griebner, Brian ;
Watts, Arthur ;
Gao, Shan ;
Pourcher, Emmanuelle ;
Bond, Louisette ;
Kompoliti, Katie ;
Agarwal, Pinky ;
Sia, Cherissa ;
Jog, Mandar ;
Cole, Linda ;
Sultana, Munira ;
Kurlan, Roger ;
Richard, Irene ;
Deeley, Cheryl ;
Waters, Cheryl H. ;
Figueroa, Angel ;
Arkun, Ani ;
Brodsky, Matthew ;
Ondo, William G. ;
Hunter, Christine B. ;
Jimenez-Shahed, Joohi ;
Palao, Alicia ;
Miyasaki, Janis M. ;
Julie, S. O. ;
Tetrud, James ;
Reys, Liza ;
Smith, Katharine ;
Singer, Carlos ;
Blenke, Anita ;
Russell, David S. ;
Cotto, Candace ;
Friedman, Joseph H. ;
Lannon, Margaret ;
Zhang, Lin ;
Drasby, Edward ;
Kumar, Rajeev .
JAMA NEUROLOGY, 2014, 71 (05) :543-552
[6]   Mitochondrial damage-associated inflammation highlights biomarkers in PRKN/PINK1 parkinsonism [J].
Borsche, Max ;
Koenig, Inke R. ;
Delcambre, Sylvie ;
Petrucci, Simona ;
Balck, Alexander ;
Brueggemann, Norbert ;
Zimprich, Alexander ;
Wasner, Kobi ;
Pereira, Sandro L. ;
Avenali, Micol ;
Deuschle, Christian ;
Badanjak, Katja ;
Ghelfi, Jenny ;
Gasser, Thomas ;
Kasten, Meike ;
Rosenstiel, Philip ;
Lohmann, Katja ;
Brockmann, Kathrin ;
Valente, Enza Maria ;
Youle, Richard J. ;
Gruenewald, Anne ;
Klein, Christine .
BRAIN, 2020, 143 :3041-3051
[7]   Basic Science Breaks Through: New Therapeutic Advances in Parkinson's Disease [J].
Brundin, Patrik ;
Atkin, Graham ;
Lamberts, Jennifer T. .
MOVEMENT DISORDERS, 2015, 30 (11) :1521-1527
[8]   Randomized phase I clinical trial of anti-α-synuclein antibody BIIB054 [J].
Brys, Miroslaw ;
Fanning, Laura ;
Hung, Serena ;
Ellenbogen, Aaron ;
Penner, Natalia ;
Yang, Minhua ;
Welch, Mackenzie ;
Koenig, Erica ;
David, Eric ;
Fox, Tara ;
Makh, Shavy ;
Aldred, Jason ;
Goodman, Ira ;
Pepinsky, Blake ;
Liu, YuTing ;
Graham, Danielle ;
Weihofen, Andreas ;
Cedarbaum, Jesse M. .
MOVEMENT DISORDERS, 2019, 34 (08) :1154-1163
[9]   Immunotherapy in Parkinson's disease: Current status and future directions [J].
Chatterjee, Diptaman ;
Kordower, Jeffrey H. .
NEUROBIOLOGY OF DISEASE, 2019, 132
[10]   Efficacy of fecal microbiota transplantation in patients with Parkinson's disease: clinical trial results from a randomized, placebo-controlled design [J].
Cheng, Yi ;
Tan, Guohua ;
Zhu, Qihui ;
Wang, Chun ;
Ruan, Guangcong ;
Ying, Senhong ;
Qie, Jinlong ;
Hu, Xiaofei ;
Xiao, Zhifeng ;
Xu, Fenghua ;
Chen, Lu ;
Chen, Minjia ;
Pei, Yang ;
Zhang, Hao ;
Tian, Yuting ;
Chen, Dongfeng ;
Liu, Xingyin ;
Huang, Heqing ;
Wei, Yanling .
GUT MICROBES, 2023, 15 (02)