Impact of Lipid Tail Length on the Organ Selectivity of mRNA-Lipid Nanoparticles

被引:2
作者
Hashiba, Kazuki [1 ]
Taguchi, Masamitsu [1 ]
Sakamoto, Sachiko [1 ]
Otsu, Ayaka [1 ]
Maeda, Yoshiki [1 ]
Suzuki, Yuichi [2 ]
Ebe, Hirofumi [1 ]
Okazaki, Arimichi [1 ]
Harashima, Hideyoshi [2 ]
Sato, Yusuke [2 ]
机构
[1] Nitto Denko Corp, Nucl Acid Med Business Div, 1-1-2 Shimohozumi, Ibaraki, Osaka 5678680, Japan
[2] Hokkaido Univ, Fac Pharmaceut Sci, Lab Mol Design Pharmaceut, Sapporo 0600812, Japan
关键词
mRNA delivery; lipid nanoparticles; ionizablelipids; endogenous targeting; immune cell; vaccine; IN-VIVO; DELIVERY; EXPRESSION; KINETICS;
D O I
10.1021/acs.nanolett.4c02566
中图分类号
O6 [化学];
学科分类号
0703 ;
摘要
The delivery of mRNA molecules to organs beyond the liver is valuable for therapeutic applications. Functionalized lipid nanoparticles (LNPs) using exogenous mechanisms can regulate in vivo mRNA expression profiles from hepatocytes to extrahepatic tissues but lead to process complexity and cost escalation. Here, we report that mRNA expression gradually shifts from the liver to the spleen in an ionizable lipid tail length-dependent manner. Remarkably, this simple chemical strategy held true even when different ionizable lipid head structures were employed. As a potential mechanism underlying this discovery, our data suggest that 1,2-distearoyl-sn-glycero-3-phosphocholine (DSPC) is enriched on the surface of mRNA/LNPs with short-tail lipids. This feature limits their interaction with biological components, avoiding their rapid hepatic clearance. We also show that spleen-targeting LNPs loaded with SARS-CoV-2 receptor-binding domain (RBD) mRNA can efficiently induce immune responses and neutralize activity following intramuscular vaccination priming and boosting.
引用
收藏
页码:12758 / 12767
页数:10
相关论文
共 50 条
[11]   Selective organ targeting (SORT) nanoparticles for tissue-specific mRNA delivery and CRISPR-Cas gene editing [J].
Cheng, Qiang ;
Wei, Tuo ;
Farbiak, Lukas ;
Johnson, Lindsay T. ;
Dilliard, Sean A. ;
Siegwart, Daniel J. .
NATURE NANOTECHNOLOGY, 2020, 15 (04) :313-+
[12]   Ionizable Amino Lipids Distribution and Effects on DSPC/Cholesterol Membranes: Implications for Lipid Nanoparticle Structure [J].
Dehghani-Ghahnaviyeh, Sepehr ;
Smith, Michael ;
Xia, Yan ;
Dousis, Athanasios ;
Grossfield, Alan ;
Sur, Sreyoshi .
JOURNAL OF PHYSICAL CHEMISTRY B, 2023, 127 (31) :6928-6939
[13]   Biodistribution and Non-linear Gene Expression of mRNA LNPs Affected by Delivery Route and Particle Size [J].
Di, Jiaxing ;
Du, Zhili ;
Wu, Kangzeng ;
Jin, Shanshan ;
Wang, Xun ;
Li, Tonglei ;
Xu, Yuhong .
PHARMACEUTICAL RESEARCH, 2022, 39 (01) :105-114
[14]   On the mechanism of tissue-specific mRNA delivery by selective organ targeting nanoparticles [J].
Dilliard, Sean A. ;
Cheng, Qiang ;
Siegwart, Daniel J. .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2021, 118 (52)
[15]   A bird's eye view on the role of dendritic cells in SARS-CoV-2 infection: Perspectives for immune-based vaccines [J].
Galati, Domenico ;
Zanotta, Serena ;
Capitelli, Ludovica ;
Bocchino, Marialuisa .
ALLERGY, 2022, 77 (01) :100-110
[16]  
Gallud A., 2021, BIOPHYSICS-USSR, DOI [10.1101/2021.08.20.457104, DOI 10.1101/2021.08.20.457104]
[17]   Ligand-tethered lipid nanoparticles for targeted RNA delivery to treat liver fibrosis [J].
Han, Xuexiang ;
Gong, Ningqiang ;
Xue, Lulu ;
Billingsley, Margaret M. ;
El-Mayta, Rakan ;
Shepherd, Sarah J. ;
Alameh, Mohamad-Gabriel ;
Weissman, Drew ;
Mitchell, Michael J. .
NATURE COMMUNICATIONS, 2023, 14 (01)
[18]   An ionizable lipid toolbox for RNA delivery [J].
Han, Xuexiang ;
Zhang, Hanwen ;
Butowska, Kamila ;
Swingle, Kelsey L. ;
Alameh, Mohamad-Gabriel ;
Weissman, Drew ;
Mitchell, Michael J. .
NATURE COMMUNICATIONS, 2021, 12 (01)
[19]   Overcoming thermostability challenges in mRNA-lipid nanoparticle systems with piperidine-based ionizable lipids [J].
Hashiba, Kazuki ;
Taguchi, Masamitsu ;
Sakamoto, Sachiko ;
Otsu, Ayaka ;
Maeda, Yoshiki ;
Ebe, Hirofumi ;
Okazaki, Arimichi ;
Harashima, Hideyoshi ;
Sato, Yusuke .
COMMUNICATIONS BIOLOGY, 2024, 7 (01)
[20]   Branching Ionizable Lipids Can Enhance the Stability, Fusogenicity, and Functional Delivery of mRNA [J].
Hashiba, Kazuki ;
Sato, Yusuke ;
Taguchi, Masamitsu ;
Sakamoto, Sachiko ;
Otsu, Ayaka ;
Maeda, Yoshiki ;
Shishido, Takuya ;
Murakawa, Masao ;
Okazaki, Arimichi ;
Harashima, Hideyoshi .
SMALL SCIENCE, 2023, 3 (01)