The Past, the Present, and the Future of Genomic Therapies in Cardiovascular Disease

被引：1
|
作者：
Mcnally, Elizabeth M. [1 ]
Puckelwartz, Megan J. [1 ]
Nobrega, Marcelo A. [2 ]
机构：
[1] Northwestern Univ, Ctr Genet Med, Feinberg Sch Med, 303 E Superior St, Chicago, IL 60611 USA
[2] Univ Chicago, Chicago, IL USA
来源：
JOURNAL OF THE AMERICAN HEART ASSOCIATION | 2024年 / 13卷 / 23期
基金：
美国国家卫生研究院;
关键词：
CRISPR; gene therapy; genetic correction; noncoding regions; upregulation; HYPERTROPHIC CARDIOMYOPATHY; VARIANTS;
D O I：
10.1161/JAHA.124.035987
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：5
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