Development of a Next-Generation Non-Viral Human FVIII Therapeutic Administered through Targeted Transcutaneous Ultrasound Enables Normal Physiological Levels of FVIII Transgene Expression in a Redosable and Titratable Manner

被引：0

|

作者：

Krivega, Margarita ^{[1
]}

Poniatowski, Julia ^{[1
]}

Kim, David ^{[1
]}

Del Greco, Elizabeth ^{[1
]}

Krivega, Ivan ^{[1
]}

Rao, Surabhi ^{[1
]}

Foster, Victor ^{[1
]}

Frederich, Bert ^{[1
]}

Campbell, Barry ^{[1
]}

Alonso, Adel ^{[1
]}

Arauz, Glenda ^{[1
]}

Ortiz, Celia ^{[1
]}

Chen, Oliver ^{[1
]}

Bole, Dhruv ^{[1
]}

Benthall, Katie ^{[1
]}

He, Charlotte ^{[1
]}

Rao, Anagha ^{[1
]}

Satyadi, David ^{[1
]}

Gluzman-Poltorak, Zoya ^{[1
]}

Feinstein, Steven B. ^{[1
]}

Greenberg, Kenneth P. ^{[1
]}

机构：

[1] SonoThera, South San Francisco, CA USA

来源：

MOLECULAR THERAPY | 2024年 / 32卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

1229.

引用

收藏

页码：585 / 586

页数：2

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