Exon 45 skipping and dystrophin production with ENTR-601-45 in preclinical models of Duchenne muscular dystrophy

被引：0
|
作者：
Girgenrath, M. [1 ]
Estrella, N. [1 ]
Kumar, A. [1 ]
Hicks, A. [1 ]
Brennan, C. [1 ]
Blake, S. [1 ]
Li, X. [1 ]
Pathak, A. [1 ]
Kheirabadi, M. [1 ]
Dougherty, P. [1 ]
Lian, W. [1 ]
Liu, N. [1 ]
Gao, N. [1 ]
Wang, D. [1 ]
Streeter, M. [1 ]
Stadheim, A. [1 ]
Dhanabal, M. [1 ]
Qian, Z. [1 ]
机构：
[1] Entrada Therapeut, Boston, MA USA
来源：
NEUROMUSCULAR DISORDERS | 2024年 / 43卷
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中图分类号：
R74 [神经病学与精神病学];
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摘要：
431P
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页数：2
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