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- [1] Exon Skipping and Dystrophin Production with ENTR-601-45, a Novel EEV-Conjugated, Exon 45 Skip Amenable PMO in Preclinical Models of DMDMOLECULAR THERAPY, 2023, 31 (04) : 637 - 637Qian, Ziqing Leo论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAEstrella, Nelsa L.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAHicks, Amy N.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAKumar, Ajay论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAGuan, Avery论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USABlake, Sara论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USACheon, Scarlett论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USALi, Xiang论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAPathak, Anushree论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAKheirabadi, Mahboubeh论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USADougherty, Patrick G.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USALian, Wenlong论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USALiu, Nanjun论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAGao, Ningguo论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAWang, Daniel论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAStreeter, Matthew论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USADhanabal, Mohanraj论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAGirgenrath, Mahasweta论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USASethuraman, Natarajan论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USA
- [2] Eteplirsen treatment for Duchenne muscular dystrophy Exon skipping and dystrophin productionNEUROLOGY, 2018, 90 (24) : E2146 - E2154Charleston, Jay S.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USASchnell, Frederick J.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USADworzak, Johannes论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USADonoghue, Cas论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USALewis, Sarah论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USAChen, Lei论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USAYoung, G. David论文数: 0 引用数: 0 h-index: 0机构: Flagship Biosci, Westminster, CO USA Sarepta Therapeut Inc, Cambridge, MA 02142 USAMilici, Anthony J.论文数: 0 引用数: 0 h-index: 0机构: Flagship Biosci, Westminster, CO USA Sarepta Therapeut Inc, Cambridge, MA 02142 USAVoss, Jon论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USADeAlwis, Uditha论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USAWentworth, Bruce论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USARodino-Klapac, Louise R.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USASahenk, Zarife论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USAFrank, Diane论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA 02142 USA Sarepta Therapeut Inc, Cambridge, MA 02142 USAMendell, Jerry R.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA 02142 USA
- [3] Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editorsMOLECULAR THERAPY-NUCLEIC ACIDS, 2023, 33 : 572 - 586Gapinske, Michael论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAWinter, Jackson论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USASwami, Devyani论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAGapinske, Lauren论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Nick J Holonyak Micro & Nano Technol Lab, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAWoods, Wendy S.论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAShirguppe, Shraddha论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAMiskalis, Angelo论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USABusza, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAJoulani, Dana论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAKao, Collin J.论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAKostan, Kurt论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA论文数: 引用数: h-index:机构:Bashir, Rashid论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Univ Illinois, Nick J Holonyak Micro & Nano Technol Lab, Urbana, IL 61801 USA Carle Illinois Coll Med, Champaign, IL 61820 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USAPerez-Pinera, Pablo论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA Carle Illinois Coll Med, Champaign, IL 61820 USA Univ Illinois, Carl R Woese Inst Genom Biol, Urbana, IL 61801 USA Univ Illinois, Canc Ctr Illinois, Urbana, IL 61801 USA Univ Illinois, Dept Mol & Integrat Physiol, Urbana, IL 61801 USA Univ Illinois, Dept Bioengn, 1406 West Green St, Urbana, IL 61801 USA
- [4] Endosomal Escape Vehicles (EEV™) - Oligonucleotides conjugates produce exon skipping and dystrophin production in preclinical models of Duchenne muscular dystrophyNEUROMUSCULAR DISORDERS, 2023, 33 : S102 - S102Girgenrath, M.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAEstrella, N.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAKumar, A.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USALi, J.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAHicks, A.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USABrennan, C.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USABlake, S.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAGuan, A.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USALi, X.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAPathak, A.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAKheirabadi, M.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USADougherty, P.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USALian, W.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USALiu, N.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAGao, N.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAWang, D.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAStreeter, M.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAStadheim, A.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USADhanabal, M.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USAQian, Z.论文数: 0 引用数: 0 h-index: 0机构: Entrada Therapeut, Boston, MA USA Entrada Therapeut, Boston, MA USA
- [5] Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophyBMC Medical Genomics, 4Dwi U Kemaladewi论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsWillem MH Hoogaars论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsSandra H van Heiningen论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsSamuel Terlouw论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsDavid JJ de Gorter论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsJohan T den Dunnen论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsGert Jan B van Ommen论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsAnnemieke Aartsma-Rus论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsPeter ten Dijke论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical GeneticsPeter AC 't Hoen论文数: 0 引用数: 0 h-index: 0机构: Leiden University Medical Center,Center for Human and Clinical Genetics
- [6] Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophyBMC MEDICAL GENOMICS, 2011, 4Kemaladewi, Dwi U.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Dept Mol & Cell Biol, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, NetherlandsHoogaars, Willem M. H.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlandsvan Heiningen, Sandra H.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, NetherlandsTerlouw, Samuel论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlandsde Gorter, David J. J.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Dept Mol & Cell Biol, NL-2300 RC Leiden, Netherlands Univ Munster, Inst Mol Cell Biol, D-48149 Munster, Germany Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlandsden Dunnen, Johan T.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlandsvan Ommen, Gert Jan B.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, NetherlandsAartsma-Rus, Annemieke论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlandsten Dijke, Peter论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Dept Mol & Cell Biol, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands't Hoen, Peter A. C.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands Leiden Univ, Med Ctr, Ctr Human & Clin Genet, NL-2300 RC Leiden, Netherlands
- [7] AOC 1044 induces exon 44 skipping and restores dystrophin protein in preclinical models of Duchenne muscular dystrophyNUCLEIC ACIDS RESEARCH, 2025, 53 (06)Etxaniz, Usue论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAMarks, Isaac论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAAlbin, Tyler论文数: 0 引用数: 0 h-index: 0机构: Seawolf Therapeut, 9880 Campus Point Dr,Suite 210, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USADiaz, Matthew论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USABhardwaj, Raghav论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, 75 Ames St, Cambridge, MA 02142 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAAnderson, Aaron论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USATyaglo, Olecya论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAHoang, Tiffany论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAMissinato, Maria Azzurra论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USASvensson, Kristoffer论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USABadillo, Ben论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAKovach, Philip R.论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USALeung, Laura论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USACochran, Michael论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAKwon, Hae Won论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAAhad Shah, Md Nur论文数: 0 引用数: 0 h-index: 0机构: Univ Alberta, Dept Med Genet, Yokota Lab, Edmonton T6G 2H, AB, Canada Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAMaruyama, Rika论文数: 0 引用数: 0 h-index: 0机构: Univ Alberta, Dept Med Genet, Yokota Lab, Edmonton T6G 2H, AB, Canada Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA论文数: 引用数: h-index:机构:Doppalapudi, Venkata R.论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USADarimont, Beatrice论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAYounis, Husam S.论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAFlanagan, W. Michael论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USALevin, Arthur A.论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAHuang, Hanhua论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USAKaramanlidis, Georgios论文数: 0 引用数: 0 h-index: 0机构: Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA Avid Biosci Inc, 10578 Sci Dr,Suite 125, San Diego, CA 92121 USA
- [8] Assessment of the feasibility of exon 45-55 multiexon skipping for duchenne muscular dystrophyBMC MEDICAL GENETICS, 2008, 9van Vliet, Laura论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlands Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlandsde Winter, Christa L.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlands Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlandsvan Deutekom, Judith C. T.论文数: 0 引用数: 0 h-index: 0机构: Prosensa Therapeut BV, NL-2333 AL Leiden, Netherlands Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlandsvan Ommen, Gert-Jan B.论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlands Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, NetherlandsAartsma-Rus, Annemieke论文数: 0 引用数: 0 h-index: 0机构: Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlands Leiden Univ, Dept Human Genet, DMD Genet Therapy Grp, Med Ctr, NL-2300 RC Leiden, Netherlands
- [9] CRISPR Base Editing Approach to Treat Duchenne Muscular Dystrophy by Skipping DMD Exon 45MOLECULAR THERAPY, 2023, 31 (04) : 609 - 609Swami, Devyani论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAGapinske, Michael论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAWinter, Jackson S.论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAGapinske, Lauren论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Nick J Holonyak Micro & Nano Technol Lab, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAWoods, Wendy S.论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAShirguppe, Shraddha论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAMiskalis, Angelo论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USABusza, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAJoulani, Dana论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAKao, Colin论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAKostan, Kurt A.论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USABashir, Rashid论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Nick J Holonyak Micro & Nano Technol Lab, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USAPerez-Pinera, Pablo论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Bioengn, Urbana, IL USA Univ Illinois, Nick J Holonyak Micro & Nano Technol Lab, Urbana, IL USA Univ Illinois, Bioengn, Urbana, IL USA
- [10] Exon skipping in Duchenne muscular dystrophyNEUROMUSCULAR DISORDERS, 2008, 18 (05) : 431 - 432Wilton, Steve论文数: 0 引用数: 0 h-index: 0机构: Univ Western Australia, Fac Med Dent & Hlth Sci, Ctr Neuromuscular & Neurol Disorders, Perth, WA, Australia Univ Western Australia, Fac Med Dent & Hlth Sci, Ctr Neuromuscular & Neurol Disorders, Perth, WA, Australia