In vivo direct bone targeting lentiviral gene therapy for MPS IVA murine model

被引：0
|
作者：
Celik, Betul [1 ]
Saikia, Sampurna [1 ]
Nidhi, Fnu [1 ]
Khan, Shaukat [2 ]
Tomatsu, Shunji [2 ]
Audi, Jennifer
Siffel, Csaba
Ayodele, Olulade
Byrne, Barry J.
Castelli, Jeffrey
Jain, Vipul
Das, Sheela Sitaraman
Zhang, Jennifer
机构：
[1] Univ Delaware, Newark, DE USA
[2] Nemours Childrens Hosp, Wilmington, DE USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2025年 / 144卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2024.108676
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
49
引用
收藏
页数：2
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