All-in-one lentiviral vectors improving bone abnormalities in MPS IVA mice

被引：0
|
作者：
Celik, Betul [1 ]
Saikia, Sampurna [1 ]
Nidhi, Fnu [1 ]
Khan, Shaukat [2 ]
Tomatsu, Shunji [2 ]
机构：
[1] Univ Delaware, Newark, DE USA
[2] Nemours Childrens Hosp, Wilmington, DE USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2025年 / 144卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2024.108675
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
48
引用
收藏
页数：2
相关论文
共 50 条
  • [1] TetR-regulated all-in-one Lentiviral vectors for conditional expression in human stem cells
    Benabdellah, K.
    Munoz, P.
    Gutierrez-Rodriguez, A.
    Cobo, M.
    Garcia-Perez, A.
    Martin, F.
    HUMAN GENE THERAPY, 2013, 24 (12) : A74 - A74
  • [2] Tightly regulated 'all-in-one' lentiviral vectors for protection of human hematopoietic cells from anticancer chemotherapy
    Lachmann, N.
    Brennig, S.
    Hillje, R.
    Schermeier, H.
    Phaltane, R.
    Dahlmann, J.
    Gruh, I.
    Heinz, N.
    Schiedlmeier, B.
    Baum, C.
    Moritz, T.
    GENE THERAPY, 2015, 22 (11) : 883 - 892
  • [3] Tightly regulated ‘all-in-one’ lentiviral vectors for protection of human hematopoietic cells from anticancer chemotherapy
    N Lachmann
    S Brennig
    R Hillje
    H Schermeier
    R Phaltane
    J Dahlmann
    I Gruh
    N Heinz
    B Schiedlmeier
    C Baum
    T Moritz
    Gene Therapy, 2015, 22 : 883 - 892
  • [4] In vivo direct bone targeting lentiviral gene therapy for MPS IVA murine model
    Celik, Betul
    Saikia, Sampurna
    Nidhi, Fnu
    Khan, Shaukat
    Tomatsu, Shunji
    Audi, Jennifer
    Siffel, Csaba
    Ayodele, Olulade
    Byrne, Barry J.
    Castelli, Jeffrey
    Jain, Vipul
    Das, Sheela Sitaraman
    Zhang, Jennifer
    MOLECULAR GENETICS AND METABOLISM, 2025, 144 (02)
  • [5] Development of all-in-one multicistronic Tet-On lentiviral vectors for inducible co-expression of two transgenes
    Huang, Yide
    Zhen, Ruonan
    Jiang, Meiqin
    Yang, Jie
    Yang, Yun
    Huang, Zhen
    Lin, Yao
    BIOTECHNOLOGY AND APPLIED BIOCHEMISTRY, 2015, 62 (01) : 48 - 54
  • [6] Targeted, homology-driven gene insertion in stem cells by ZFN-loaded 'all-in-one' lentiviral vectors
    Cai, Yujia
    Laustsen, Anders
    Zhou, Yan
    Sun, Chenglong
    Anderson, Mads Valdemar
    Li, Shengting
    Uldbjerg, Niels
    Luo, Yonglun
    Jakobsen, Martin R.
    Mikkelsen, Jacob Giehm
    ELIFE, 2016, 5
  • [7] Polyswitch Lentivectors: "All-in-One" Lentiviral Vectors for Drug-Inducible Gene Expression, Live Selection, and Recombination Cloning
    Giry-Laterriere, Marc
    Cherpin, Ophelie
    Kim, Yong-Sik
    Jensen, Jan
    Salmon, Patrick
    HUMAN GENE THERAPY, 2011, 22 (10) : 1255 - 1267
  • [8] Development of a new All-In-One inducible lentiviral shRNA/gRNA Vector
    Wu, Lipeng
    Su, Hua
    Fellows, Justin
    Fu, Mao
    Heller, Julian
    Park, Brian
    Yin, Dezhong
    CANCER RESEARCH, 2023, 83 (07)
  • [9] Development of a new All-In-One inducible lentiviral shRNA/gRNA Vector
    Wu, L.
    Su, H.
    Fellows, J.
    Fu, M.
    Heller, J.
    Park, B.
    Yin, D.
    MOLECULAR BIOLOGY OF THE CELL, 2023, 34 (02) : 870 - 870
  • [10] MPS-ATLAS: A fast all-in-one code for synthesising stellar spectra
    Witzke, V
    Shapiro, A., I
    Cernetic, M.
    Tagirov, R., V
    Kostogryz, N. M.
    Anusha, L. S.
    Unruh, Y. C.
    Solanki, S. K.
    Kurucz, R. L.
    ASTRONOMY & ASTROPHYSICS, 2021, 653
12345