Skeletal Damage and Cross-correction after ex-vivo Gene Therapy in Mucopolysaccharidosis type I Hurler

被引：0

作者：

Santi, Ludovica ^{[1
]}

Crippa, Stefania ^{[1
]}

Capo, Valentina ^{[1
]}

Penna, Sara ^{[1
]}

Savoia, Evelyn ^{[1
]}

De Ponti, Giada ^{[1
]}

Alberti, Gaia ^{[1
]}

Berti, Margherita ^{[1
]}

Ceriotti, Selene ^{[1
]}

Consiglieri, Giulia ^{[2
]}

Tucci, Francesca ^{[2
]}

Riminucci, Mara ^{[3
]}

Corsi, Alessandro ^{[3
]}

Barbero, Andrea ^{[4
]}

Martin, Ivan ^{[4
]}

Sanvito, Francesca ^{[5
]}

Norata, Rossana ^{[5
]}

Rocchi, Martina ^{[5
]}

Bolamperti, Simona ^{[6
]}

Villa, Isabella ^{[6
]}

Aiuti, Alessandro ^{[1
]}

Villa, Anna ^{[1
]}

Bernardo, Maria Ester ^{[1
]}

机构：

[1] San Raffaele Telethon Inst Gene Therapy, Milan, Italy

[2] IRCCS San Raffaele Sci Inst, Pediatr Immunohematol & Bone Marrow Transplantat, Milan, Italy

[3] Sapienza Univ, Dept Mol Med, Rome, Italy

[4] Univ Basel Hosp, Tissue Engn Dept Biomed, Basel, Switzerland

[5] IRCCS San Raffaele Sci Inst, GLP San Raffaele Telethon Inst Gene Therapy, Milan, Italy

[6] IRCCS San Raffaele Sci Inst, Osteoporosis & Bone & Mineral Metab Unit, Milan, Italy

来源：

JOURNAL OF BONE AND MINERAL RESEARCH | 2024年 / 39卷

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

FRI-166

引用

页码：30 / 31

页数：2

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