共 50 条
- [3] Unmet clinical needs and burden in Angelman syndrome: a review of the literature ORPHANET JOURNAL OF RARE DISEASES, 2017, 12
- [4] Unmet clinical needs and burden in Angelman syndrome: a review of the literature Orphanet Journal of Rare Diseases, 12
- [7] The humanistic burden of Pompe disease: are there still unmet needs? A systematic review BMC Neurology, 17