Reverse transcriptase inhibitors in Aicardi-Goutières syndrome: Design and regulatory challenges in clinical trials for rare disease

被引：0
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作者：
Dale, Russell C. [1 ,2 ]
机构：
[1] Univ Sydney, Paediat Neurol, Westmead, Australia
[2] Childrens Hosp Westmead, Westmead, Australia
来源：
DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY | 2025年
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D O I：
10.1111/dmcn.16237
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
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页数：2
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