Quantifying the burden-of-illness of Duchenne muscular dystrophy in Belgium: an interim analysis of a site-based survey

被引：0
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作者：
De Waele, L. [1 ,2 ]
Cremers, J. [3 ]
Debien, E. [3 ]
Gielis, E. [1 ]
Maenen, V. [1 ]
Vanoppen, I. [3 ]
Van Stappen, T. [4 ]
Beeckman, L. [4 ]
Posner, N. [5 ]
Dukacz, S. [5 ]
Jiang, L. [5 ]
Evans, J. [6 ]
Wu, Y. [6 ]
Jones, C. [6 ]
Meeus, L. [7 ]
Claeys, K. [3 ,8 ]
机构：
[1] Univ Hosp Leuven, Dept Child Neurol, Leuven, Belgium
[2] Katholieke Univ Leuven, Dept Dev & Regenerat, Leuven, Belgium
[3] Univ Hosp Leuven, Dept Neurol, Leuven, Belgium
[4] Pfizer, Brussels, Belgium
[5] Pfizer, New York, NY USA
[6] Prime HCD, London, England
[7] Duchenne Parent Project Belgium, Haacht, Belgium
[8] Katholieke Univ Leuven, Lab Muscle Dis & Neuropathies, Dept Neurosci, Leuven, Belgium
来源：
NEUROMUSCULAR DISORDERS | 2024年 / 43卷
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中图分类号：
R74 [神经病学与精神病学];
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摘要：
336P
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页数：1
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