Quantifying the burden-of-illness of Duchenne muscular dystrophy in Belgium: an interim analysis of a site-based survey

被引：0

作者：

De Waele, L. ^{[1
,2
]}

Cremers, J. ^{[3
]}

Debien, E. ^{[3
]}

Gielis, E. ^{[1
]}

Maenen, V. ^{[1
]}

Vanoppen, I. ^{[3
]}

Van Stappen, T. ^{[4
]}

Beeckman, L. ^{[4
]}

Posner, N. ^{[5
]}

Dukacz, S. ^{[5
]}

Jiang, L. ^{[5
]}

Evans, J. ^{[6
]}

Wu, Y. ^{[6
]}

Jones, C. ^{[6
]}

Meeus, L. ^{[7
]}

Claeys, K. ^{[3
,8
]}

机构：

[1] Univ Hosp Leuven, Dept Child Neurol, Leuven, Belgium

[2] Katholieke Univ Leuven, Dept Dev & Regenerat, Leuven, Belgium

[3] Univ Hosp Leuven, Dept Neurol, Leuven, Belgium

[4] Pfizer, Brussels, Belgium

[5] Pfizer, New York, NY USA

[6] Prime HCD, London, England

[7] Duchenne Parent Project Belgium, Haacht, Belgium

[8] Katholieke Univ Leuven, Lab Muscle Dis & Neuropathies, Dept Neurosci, Leuven, Belgium

来源：

NEUROMUSCULAR DISORDERS | 2024年 / 43卷

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

336P

引用

页数：1

共 47 条

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[29] Stem cell transplantation for treating Duchenne muscular dystrophy A Web of Science-based literature analysis
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[30] Stem cell transplantation for treating Duchenne muscular dystrophy A Web of Science-based literature analysis
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