Congenital Erythropoietic Porphyria: Mild and Severe Form in Two Brothers

被引:0
|
作者
Badabagni, Purnachandra [1 ]
Birudala, Ramadevi [2 ]
机构
[1] ESIC Med Coll & Hosp, Dept Dermatol Venereol & Leprosy, Hyderabad, Telangana, India
[2] Sri Balaji Med Coll & Hosp, Dept Dermatol Venereol & Leprosy, Tirupati, Andhra Pradesh, India
关键词
Congenital erythropoietic porphyria; erythrodontia; uroporphyrinogen III cosynthase;
D O I
10.4103/ijpd.ijpd_12_23
中图分类号
R75 [皮肤病学与性病学];
学科分类号
100206 ;
摘要
Congenital erythropoietic porphyria (CEP) is an autosomal recessive inherited metabolic disorder caused due to deficiency of the enzyme uroporphyrinogen III cosynthase, resulting in large amounts of type I isomers, which massively accumulate in erythroid cells and then leak into plasma. CEP clinically presents as lifelong mutilating photosensitivity, erythrodontia, and hemolytic anemia. We report two brothers born out of consanguineous marriage with a diversity of features, i.e., mild and severe variants of CEP with hemolytic anemia and supported by genetic analysis.
引用
收藏
页码:121 / 124
页数:4
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