Short-term and long-term safety profile of Givinostat in Duchenne muscular dystrophy

被引：0
|
作者：
Vucinic, D. [1 ]
Nascimento, A. [2 ]
Finkel, R. [3 ]
Brandsema, J. [4 ]
Finanger, E. [5 ]
Harper, A. [6 ]
Acsadi, G. [7 ]
Nevo, Y. [8 ]
Houwen-van Opstal, S. [9 ]
Blaschek, A. [10 ]
Coceani, N. [11 ]
Cazzaniga, S. [11 ]
Bettica, P. [11 ]
Muelas, N. [12 ]
机构：
[1] Clin Neurol & Psychiat Children & Youth, Belgrade, Serbia
[2] Hosp St Joan Deu, Neuromuscular Pathol Unit, Barcelona, Spain
[3] St Jude Childrens Res Hosp, Memphis, TN USA
[4] Childrens Hosp, Philadelphia, PA USA
[5] Shriners Hosp Children, Portland, OR USA
[6] Virginia Commonwealth Univ, Richmond, VA USA
[7] Connecticut Childrens Med Ctr, Hartford, CT USA
[8] Schneider Childrens Med Ctr, Tel Aviv, Israel
[9] Radboud Univ Nijmegen, Med Ctr, Nijmegen, Netherlands
[10] Ludwig Maximilian Univ Munic, Munic, Germany
[11] Italfarmaco Grp, Milan, Italy
[12] Hosp Univ & Politecn La Fe, Valencia, Spain
来源：
NEUROMUSCULAR DISORDERS | 2024年 / 43卷
关键词：
D O I：
10.1016/j.nmd.2024.07.289
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
409P
引用
收藏
页数：2
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