Reply to "Levacetylleucine a game changer for Niemann-Pick disease type-C"

被引：0
|
作者：
Matsuo, Muneaki [1 ]
Ishitsuka, Yoichi [2 ]
Irie, Tetsumi [2 ,3 ]
机构：
[1] Saga Univ, Fac Med, Dept Pediat, 5-1-1 Nabeshima, Saga 8498501, Japan
[2] Kumamoto Univ, Grad Sch Pharmaceut Sci, Dept Clin Chem & Informat, Kumamoto, Japan
[3] Kumamoto Univ, Fac Life Sci, Dept Pharmaceut Packaging Technol, Kumamoto, Japan
来源：
BRAIN & DEVELOPMENT | 2025年 / 47卷 / 01期
关键词：
D O I：
10.1016/j.braindev.2024.104301
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
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页数：1
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