共 8 条
[1]
Genome editing with CRISPR-Cas nucleases, base editors, transposases and prime editors
[J].
Anzalone, Andrew V.
;
Koblan, Luke W.
;
Liu, David R.
.
NATURE BIOTECHNOLOGY,
2020, 38 (07)
:824-844

Anzalone, Andrew V.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Koblan, Luke W.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Liu, David R.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
[2]
Single-dose CRISPR-Cas9 therapy extends lifespan of mice with Hutchinson-Gilford progeria syndrome
[J].
Beyret, Ergin
;
Liao, Hsin-Kai
;
Yamamoto, Mako
;
Hernandez-Benitez, Reyna
;
Fu, Yunpeng
;
Erikson, Galina
;
Reddy, Pradeep
;
Belmonte, Juan Carlos Izpisua
.
NATURE MEDICINE,
2019, 25 (03)
:419-+

Beyret, Ergin
论文数: 0 引用数: 0
h-index: 0
机构:
Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA

Liao, Hsin-Kai
论文数: 0 引用数: 0
h-index: 0
机构:
Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA

Yamamoto, Mako
论文数: 0 引用数: 0
h-index: 0
机构:
Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA
Univ Catolica San Antonio Murcia, Murcia, Spain Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA

论文数: 引用数:
h-index:
机构:

Fu, Yunpeng
论文数: 0 引用数: 0
h-index: 0
机构:
Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA

Erikson, Galina
论文数: 0 引用数: 0
h-index: 0
机构:
Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA

Reddy, Pradeep
论文数: 0 引用数: 0
h-index: 0
机构:
Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA

Belmonte, Juan Carlos Izpisua
论文数: 0 引用数: 0
h-index: 0
机构:
Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA Salk Inst Biol Studies, 10010 N Torrey Pines Rd, La Jolla, CA 92037 USA
[3]
A targeted antisense therapeutic approach for Hutchinson-Gilford progeria syndrome
[J].
Erdos, Michael R.
;
Cabral, Wayne A.
;
Tavarez, Urraca L.
;
Cao, Kan
;
Gvozdenovic-Jeremic, Jelena
;
Narisu, Narisu
;
Zerfas, Patricia M.
;
Crumley, Stacy
;
Boku, Yoseph
;
Hanson, Gunnar
;
Mourich, Dan V.
;
Kole, Ryszard
;
Eckhaus, Michael A.
;
Gordon, Leslie B.
;
Collins, Francis S.
.
NATURE MEDICINE,
2021, 27 (03)
:536-+

Erdos, Michael R.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Cabral, Wayne A.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Tavarez, Urraca L.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Cao, Kan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Maryland, Dept Cell Biol & Mol Genet, College Pk, MD 20742 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Gvozdenovic-Jeremic, Jelena
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Narisu, Narisu
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Zerfas, Patricia M.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Diagnost & Res Serv Branch, Div Vet Resources, Off Res Serv, Bldg 10, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Crumley, Stacy
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Boku, Yoseph
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Hanson, Gunnar
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Mourich, Dan V.
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon State Univ, Dept Vet Hlth Sci, Corvallis, OR 97331 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Kole, Ryszard
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, Cambridge, MA USA
Univ N Carolina, Dept Pharmacol, Chapel Hill, NC 27515 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Eckhaus, Michael A.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Diagnost & Res Serv Branch, Div Vet Resources, Off Res Serv, Bldg 10, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Gordon, Leslie B.
论文数: 0 引用数: 0
h-index: 0
机构:
Brown Univ, Dept Pediat, Hasbro Childrens Hosp, Providence, RI 02912 USA
Brown Univ, Warren Alpert Med Sch, Providence, RI 02912 USA
Boston Childrens Hosp, Dept Anesthesiol Preoperat & Pain Med, Boston, MA USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA

Collins, Francis S.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA NHGRI, Mol Genet Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA
[4]
Impact of Farnesylation Inhibitors on Survival in Hutchinson-Gilford Progeria Syndrome
[J].
Gordon, Leslie B.
;
Massaro, Joe
;
D'Agostino, Ralph B.
;
Campbell, Susan E.
;
Brazier, Joan
;
Brown, W. Ted
;
Kleinman, Monica E.
;
Kieran, Mark W.
.
CIRCULATION,
2014, 130 (01)
:27-+

Gordon, Leslie B.
论文数: 0 引用数: 0
h-index: 0
机构:
Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA
Brown Univ, Warren Alpert Med Sch, Providence, RI 02912 USA
Boston Childrens Hosp, Div Crit Care Med, Dept Anesthesia, Boston, MA USA
Harvard Univ, Sch Med, Boston, MA USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA

Massaro, Joe
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Univ, Dept Math & Stat, Harvard Clin Res Inst, Boston, MA 02215 USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA

D'Agostino, Ralph B.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Univ, Dept Math & Stat, Harvard Clin Res Inst, Boston, MA 02215 USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA

Campbell, Susan E.
论文数: 0 引用数: 0
h-index: 0
机构:
Brown Univ, Ctr Gerontol & Hlth Care Res, Providence, RI 02912 USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA

Brazier, Joan
论文数: 0 引用数: 0
h-index: 0
机构:
Brown Univ, Ctr Gerontol & Hlth Care Res, Providence, RI 02912 USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA

Brown, W. Ted
论文数: 0 引用数: 0
h-index: 0
机构:
New York State Inst Basic Res, Dept Genet, Staten Isl, NY USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA

Kleinman, Monica E.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Div Crit Care Med, Dept Anesthesia, Boston, MA USA
Harvard Univ, Sch Med, Boston, MA USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA

Kieran, Mark W.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Boston, MA USA
Boston Childrens Hosp, Div Pediat Oncol, Dana Farber Canc Inst, Boston, MA USA Hasbro Childrens Hosp, Dept Pediat, Providence, RI 02903 USA
[5]
In vivo base editing rescues Hutchinson-Gilford progeria syndrome in mice
[J].
Koblan, Luke W.
;
Erdos, Michael R.
;
Wilson, Christopher
;
Cabral, Wayne A.
;
Levy, Jonathan M.
;
Xiong, Zheng-Mei
;
Tavarez, Urraca L.
;
Davison, Lindsay M.
;
Gete, Yantenew G.
;
Mao, Xiaojing
;
Newby, Gregory A.
;
Doherty, Sean P.
;
Narisu, Narisu
;
Sheng, Quanhu
;
Krilow, Chad
;
Lin, Charles Y.
;
Gordon, Leslie B.
;
Cao, Kan
;
Collins, Francis S.
;
Brown, Jonathan D.
;
Liu, David R.
.
NATURE,
2021, 589 (7843)
:608-+

Koblan, Luke W.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Erdos, Michael R.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, NIH, Bethesda, MD 20892 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Wilson, Christopher
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Cabral, Wayne A.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, NIH, Bethesda, MD 20892 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Levy, Jonathan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Xiong, Zheng-Mei
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, NIH, Bethesda, MD 20892 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Tavarez, Urraca L.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, NIH, Bethesda, MD 20892 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Davison, Lindsay M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vanderbilt Univ, Med Ctr, Div Cardiovasc Med, Nashville, TN 37235 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Gete, Yantenew G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Maryland, Dept Cell Biol & Mol Genet, College Pk, MD 20742 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Mao, Xiaojing
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Maryland, Dept Cell Biol & Mol Genet, College Pk, MD 20742 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Newby, Gregory A.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Doherty, Sean P.
论文数: 0 引用数: 0
h-index: 0
机构:
Vanderbilt Univ, Med Ctr, Div Cardiovasc Med, Nashville, TN 37235 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Narisu, Narisu
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, NIH, Bethesda, MD 20892 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Sheng, Quanhu
论文数: 0 引用数: 0
h-index: 0
机构:
Vanderbilt Univ, Med Ctr, Dept Biostat, Nashville, TN USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Krilow, Chad
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, NIH, Bethesda, MD 20892 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Lin, Charles Y.
论文数: 0 引用数: 0
h-index: 0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Baylor Coll Med, Dept Biochem & Mol Biol, Therapeut Innovat Ctr, Houston, TX 77030 USA
Kronos Bio Inc, Cambridge, MA USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Gordon, Leslie B.
论文数: 0 引用数: 0
h-index: 0
机构:
Brown Univ, Alpert Med Sch, Hasbro Childrens Hosp, Providence, RI 02912 USA
Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Cao, Kan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Maryland, Dept Cell Biol & Mol Genet, College Pk, MD 20742 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Collins, Francis S.
论文数: 0 引用数: 0
h-index: 0
机构:
NHGRI, NIH, Bethesda, MD 20892 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Brown, Jonathan D.
论文数: 0 引用数: 0
h-index: 0
机构:
Vanderbilt Univ, Med Ctr, Div Cardiovasc Med, Nashville, TN 37235 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Liu, David R.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst Harvard & MIT, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
[6]
In vivo CRISPR base editing of PCSK9 durably lowers cholesterol in primates
[J].
Musunuru, Kiran
;
Chadwick, Alexandra C.
;
Mizoguchi, Taiji
;
Garcia, Sara P.
;
DeNizio, Jamie E.
;
Reiss, Caroline W.
;
Wang, Kui
;
Iyer, Sowmya
;
Dutta, Chaitali
;
Clendaniel, Victoria
;
Amaonye, Michael
;
Beach, Aaron
;
Berth, Kathleen
;
Biswas, Souvik
;
Braun, Maurine C.
;
Chen, Huei-Mei
;
Colace, Thomas, V
;
Ganey, John D.
;
Gangopadhyay, Soumyashree A.
;
Garrity, Ryan
;
Kasiewicz, Lisa N.
;
Lavoie, Jennifer
;
Madsen, James A.
;
Matsumoto, Yuri
;
Mazzola, Anne Marie
;
Nasrullah, Yusuf S.
;
Nneji, Joseph
;
Ren, Huilan
;
Sanjeev, Athul
;
Shay, Madeleine
;
Stahley, Mary R.
;
Fan, Steven H. Y.
;
Tam, Ying K.
;
Gaudelli, Nicole M.
;
Ciaramella, Giuseppe
;
Stolz, Leslie E.
;
Malyala, Padma
;
Cheng, Christopher J.
;
Rajeev, Kallanthottathil G.
;
Rohde, Ellen
;
Bellinger, Andrew M.
;
Kathiresan, Sekar
.
NATURE,
2021, 593 (7859)
:429-+

Musunuru, Kiran
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA
Univ Penn, Dept Med, Perelman Sch Med, Div Cardiovasc Med, Philadelphia, PA 19104 USA
Univ Penn, Perelman Sch Med, Dept Genet, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Chadwick, Alexandra C.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Mizoguchi, Taiji
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Garcia, Sara P.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

DeNizio, Jamie E.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Reiss, Caroline W.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Wang, Kui
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Iyer, Sowmya
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Dutta, Chaitali
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Clendaniel, Victoria
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Amaonye, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Beach, Aaron
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Berth, Kathleen
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Biswas, Souvik
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Braun, Maurine C.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Chen, Huei-Mei
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Colace, Thomas, V
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Ganey, John D.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Gangopadhyay, Soumyashree A.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Garrity, Ryan
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Kasiewicz, Lisa N.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Lavoie, Jennifer
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Madsen, James A.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Matsumoto, Yuri
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Mazzola, Anne Marie
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Nasrullah, Yusuf S.
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Nneji, Joseph
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Ren, Huilan
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Sanjeev, Athul
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Shay, Madeleine
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Stahley, Mary R.
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Fan, Steven H. Y.
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Acuitas Therapeut, Vancouver, BC, Canada Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Tam, Ying K.
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Acuitas Therapeut, Vancouver, BC, Canada Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Gaudelli, Nicole M.
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Beam Therapeut, Cambridge, MA USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Ciaramella, Giuseppe
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Beam Therapeut, Cambridge, MA USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Stolz, Leslie E.
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Malyala, Padma
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Cheng, Christopher J.
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Rajeev, Kallanthottathil G.
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Rohde, Ellen
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Bellinger, Andrew M.
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA

Kathiresan, Sekar
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Verve Therapeut, Cambridge, MA 02139 USA Univ Penn, Perelman Sch Med, Cardiovasc Inst, Philadelphia, PA 19104 USA
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Systematic screening identifies therapeutic antisense oligonucleotides for Hutchinson-Gilford progeria syndrome
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Puttaraju, Madaiah
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h-index: 0
机构:
NCI, NIH, Bethesda, MD 20892 USA NCI, NIH, Bethesda, MD 20892 USA

Jackson, Michaela
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h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA NCI, NIH, Bethesda, MD 20892 USA

Klein, Stephanie
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h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA NCI, NIH, Bethesda, MD 20892 USA

Shilo, Asaf
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h-index: 0
机构:
NCI, NIH, Bethesda, MD 20892 USA NCI, NIH, Bethesda, MD 20892 USA

Bennett, C. Frank
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机构:
Ionis Pharmaceut, Carlsbad, CA USA NCI, NIH, Bethesda, MD 20892 USA

Gordon, Leslie
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h-index: 0
机构:
Brown Univ, Dept Pediat, Hasbro Childrens Hosp, Div Genet, Providence, RI 02912 USA
Brown Univ, Warren Alpert Med Sch, Providence, RI 02912 USA
Boston Childrens Hosp, Dept Anesthesiol Perioperat & Pain Med, Boston, MA USA
Harvard Med Sch, Boston, MA 02115 USA NCI, NIH, Bethesda, MD 20892 USA

Rigo, Frank
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h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA NCI, NIH, Bethesda, MD 20892 USA

Misteli, Tom
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NCI, NIH, Bethesda, MD 20892 USA NCI, NIH, Bethesda, MD 20892 USA
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Rolas, Loic
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Barkaway, Anna
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Santiago-Fernandez, Olaya
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机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Osorio, Fernando G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Quesada, Victor
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain
Ctr Invest Biomed Red Canc, Madrid, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Rodriguez, Francisco
论文数: 0 引用数: 0
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机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Basso, Sammy
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Maeso, Daniel
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Rolas, Loic
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h-index: 0
机构:
Queen Mary Univ London, Barts & London Sch Med & Dent, William Harvey Res Inst, London, England Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

论文数: 引用数:
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机构:

Nourshargh, Sussan
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h-index: 0
机构:
Queen Mary Univ London, Barts & London Sch Med & Dent, William Harvey Res Inst, London, England Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Folgueras, Alicia R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Freije, Jose M. P.
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h-index: 0
机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain
Ctr Invest Biomed Red Canc, Madrid, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain

Lopez-Otin, Carlos
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain
Ctr Invest Biomed Red Canc, Madrid, Spain Univ Oviedo, Fac Med, Dept Bioquim & Biol Mol, Inst Univ Oncol Principado Asturias, Oviedo, Spain