Natural history of bone health in Duchenne muscular dystrophy: A systematic review and implications for the design of a clinical trial

被引:0
作者
De Ford, C. [1 ]
Guridi, M. [1 ]
Chen, Y. [2 ]
Murphy, A. [3 ]
Wood, C. [4 ]
McMillan, H. [5 ]
Mercuri, E. [6 ,7 ]
Crabtree, N. [8 ]
Ward, L. [9 ,10 ]
机构
[1] F Hoffmann La Roche Ltd, Basel, Switzerland
[2] Genentech Inc, 460 Point San Bruno Blvd, San Francisco, CA 94080 USA
[3] Roche Prod Ltd, Welwyn Garden City AL7 3AY, Herts, England
[4] Royal Victoria Infirm, Dept Paediat Endocrinol, Newcastle Upon Tyne, Tyne & Wear, England
[5] Univ Ottawa, Childrens Hosp Eastern Ontario, Div Neurol, Dept Pediat, Ottawa, ON, Canada
[6] Catholic Univ, Pediat Neurol Inst, Rome, Italy
[7] Fdn Policlin Gemelli IRCCS, Nemo Pediat, Rome, Italy
[8] Birmingham Womens & Childrens NHS Fdn Trust, Birmingham, W Midlands, England
[9] Univ Ottawa, Childrens Hosp Eastern Ontario, Div Endocrinol, Dept Pediat, Ottawa, ON, Canada
[10] Childrens Hosp Eastern Ontario, Res Inst, Ottawa Pediat Bone Hlth Res Grp, Ottawa, ON, Canada
关键词
D O I
10.1016/j.nmd.2024.07.126
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
389P
引用
收藏
页数:1
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