NEUROPATHY IMPAIRMENT AND NUTRITIONAL STATUS WITH EPLONTERSEN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS

被引：0
|
作者：
Conceicao, Isabel [1 ]
Wixner, Jonas [2 ]
Berk, John [3 ]
Adams, David [4 ]
Polydefkis, Michael [5 ]
Attarian, Shahram [6 ]
Gillmore, Julian [7 ]
Dyck, P. James [8 ]
Coelho, Teresa [9 ,10 ]
Chen, Jersey [11 ]
Hardy, Elise [11 ]
Kwoh, Jesse [12 ]
Natman, Jonatan [13 ]
Cruz, Marcia Waddington [14 ]
机构：
[1] Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, Portugal
[2] Umea Univ, Umea, Sweden
[3] Boston Univ, Sch Med, Boston, MA USA
[4] Hop Bicetre, Le Kremlin Bicetre, France
[5] Johns Hopkins Univ, Baltimore, MD USA
[6] Ctr Hosp Univ La Timone, Neuromuscular Disorders & ALS Dept, Marseille, France
[7] UCL, Natl Amyloidosis Ctr, London, England
[8] Mayo Clin, Dept Neurol, Rochester, MN USA
[9] Ctr Hosp Univ Santo Antonio, Porto, Portugal
[10] ERN NMD, Paris, France
[11] AstraZeneca, Late Stage Dev Cardiovasc Renal & Metab, BioPharmaceut R&D, Gaithersburg, MD USA
[12] Ionis Pharmaceut Inc, Carlsbad, CA USA
[13] AstraZeneca, Global Evidence, BioPharmaceut Med, Gothenburg, Sweden
[14] Univ Fed Rio de Janeiro, Amyloidosis Ctr, CEPARM, Univ Hosp, Rio De Janeiro, Brazil
来源：
JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2024年 / 29卷
关键词：
Amyloid; ATTRv; eplontersen; polyneuropathy; transthyretin amyloidosis;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P 319
引用
收藏
页码：S138 / S138
页数：1
相关论文
共 50 条
  • [31] Inotersen for the treatment of adults with polyneuropathy caused by hereditary transthyretin-mediated amyloidosis
    Gertz, Morie A.
    Scheinberg, Morton
    Waddington-Cruz, Marcia
    Heitner, Stephen B.
    Karam, Chafic
    Drachman, Brian
    Khella, Sami
    Whelan, Carol
    Obici, Laura
    EXPERT REVIEW OF CLINICAL PHARMACOLOGY, 2019, 12 (08) : 701 - 711
  • [32] The impact of inotersen on Neuropathy Impairment Score in patients with hereditary transthyretin amyloidosis with polyneuropathy
    Aaron Yarlas
    Andrew Lovley
    Duncan Brown
    Montserrat Vera-Llonch
    Sami Khella
    Chafic Karam
    BMC Neurology, 23
  • [33] The impact of inotersen on Neuropathy Impairment Score in patients with hereditary transthyretin amyloidosis with polyneuropathy
    Yarlas, Aaron
    Lovley, Andrew
    Brown, Duncan
    Vera-Llonch, Montserrat
    Khella, Sami
    Karam, Chafic
    BMC NEUROLOGY, 2023, 23 (01)
  • [34] Switching from inotersen to eplontersen in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: analysis from NEURO-TTRansform (vol 271, pg 6655, 2024)
    Conceicao, Isabel
    Berk, John L.
    Weiler, Markus
    Kowacs, Pedro A.
    Dasgupta, Noel R.
    Khella, Sami
    Chao, Chi-Chao
    Attarian, Shahram
    Kwoh, T. Jesse
    Jung, Shiangtung W.
    Chen, Jersey
    Viney, Nicholas J.
    Yu, Rosie Z.
    Gertz, Morie
    Masri, Ahmad
    Cruz, Marcia Waddington
    Coelho, Teresa
    JOURNAL OF NEUROLOGY, 2025, 272 (02)
  • [35] Longitudinal changes in mNIS+7 are associated with changes in ambulatory status in hereditary transthyretin-mediated amyloidosis
    Coelho, Teresa
    Suhr, Ole
    Quan, Dianna
    Brannagan, Thomas
    Gollob, Jared
    Goyal, Sunita
    Altincatal, Arman
    Agarwal, Sonalee
    Lin, Hollis
    Adams, David
    JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2018, 23 (04) : 354 - 355
  • [36] Identifying Mixed Phenotype: Evaluating the Presence of Polyneuropathy in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Cardiomyopathy
    Grogan, Martha
    Hawkins, Philip N.
    Kristen, Arnt V.
    Berk, John L.
    Suhr, Ole B.
    Lin, Hollis
    Merkel, Madeline
    McManus, Anastasia
    Powell, Christine
    Vest, John
    Karsten, Verena
    Judge, Daniel P.
    JOURNAL OF CARDIAC FAILURE, 2019, 25 (08) : S9 - S10
  • [37] HELIOS-A: IMPACT OF VUTRISIRAN ON QUALITY OF LIFE AND FUNCTIONAL STATUS IN HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
    Ajroud-Driss, Senda
    Berk, John
    Adams, David
    Gillmore, Julian D.
    Lin, Kon-Ping
    Kale, Parag
    Koike, Haruki
    Aldinc, Emre
    Chen, Chongshu
    Vest, John
    Obici, Laura
    JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2022, 27 : S6 - S6
  • [38] Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
    Obici, Laura
    Ajroud-Driss, Senda
    Lin, Kon-Ping
    Berk, John L.
    Gillmore, Julian D.
    Kale, Parag
    Koike, Haruki
    Danese, David
    Aldinc, Emre
    Chen, Chongshu
    Vest, John
    Adams, David
    NEUROLOGY AND THERAPY, 2023, 12 (05) : 1759 - 1775
  • [39] Long-term Integrated Safety of Patisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
    Gillmore, Julian
    Berk, John
    Dispenzieri, Angela
    Polydefkis, Michael
    Gonzalez-Duarte, Alejandra
    Sekijima, Yoshiki
    Sweetser, Marianne T.
    Arum, Seth
    Wang, Jing Jing
    White, Matthew T.
    Maurer, Mathew
    JOURNAL OF CARDIAC FAILURE, 2020, 26 (10) : S67 - S68
  • [40] LONGTERM TREATMENT EFFECTS OF INOTERSEN ON QUALITY OF LIFE IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
    Brown, Duncan
    Karam, Chafic
    Yang, Min
    Done, Nicolae
    Zhu, JingJing
    Greatsinger, Ali
    Bozas, Ana
    Llonch, Montserrat Vera
    Signorovitch, James
    MUSCLE & NERVE, 2021, 64 : S57 - S57
12345