NEUROPATHY IMPAIRMENT AND NUTRITIONAL STATUS WITH EPLONTERSEN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS

被引：0
|
作者：
Conceicao, Isabel [1 ]
Wixner, Jonas [2 ]
Berk, John [3 ]
Adams, David [4 ]
Polydefkis, Michael [5 ]
Attarian, Shahram [6 ]
Gillmore, Julian [7 ]
Dyck, P. James [8 ]
Coelho, Teresa [9 ,10 ]
Chen, Jersey [11 ]
Hardy, Elise [11 ]
Kwoh, Jesse [12 ]
Natman, Jonatan [13 ]
Cruz, Marcia Waddington [14 ]
机构：
[1] Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, Portugal
[2] Umea Univ, Umea, Sweden
[3] Boston Univ, Sch Med, Boston, MA USA
[4] Hop Bicetre, Le Kremlin Bicetre, France
[5] Johns Hopkins Univ, Baltimore, MD USA
[6] Ctr Hosp Univ La Timone, Neuromuscular Disorders & ALS Dept, Marseille, France
[7] UCL, Natl Amyloidosis Ctr, London, England
[8] Mayo Clin, Dept Neurol, Rochester, MN USA
[9] Ctr Hosp Univ Santo Antonio, Porto, Portugal
[10] ERN NMD, Paris, France
[11] AstraZeneca, Late Stage Dev Cardiovasc Renal & Metab, BioPharmaceut R&D, Gaithersburg, MD USA
[12] Ionis Pharmaceut Inc, Carlsbad, CA USA
[13] AstraZeneca, Global Evidence, BioPharmaceut Med, Gothenburg, Sweden
[14] Univ Fed Rio de Janeiro, Amyloidosis Ctr, CEPARM, Univ Hosp, Rio De Janeiro, Brazil
来源：
JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2024年 / 29卷
关键词：
Amyloid; ATTRv; eplontersen; polyneuropathy; transthyretin amyloidosis;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P 319
引用
收藏
页码：S138 / S138
页数：1
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