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- [32] Impact of Patisiran, an RNAi Therapeutic, on Diarrhea Symptoms in Patients With Hereditary Transthyretin-Mediated Amyloidosis AMERICAN JOURNAL OF GASTROENTEROLOGY, 2020, 115 : S1657 - S1657
- [37] Patisiran for the Treatment of Transthyretin-mediated Amyloidosis with Cardiomyopathy HEART INTERNATIONAL, 2023, 17 (01): : 27 - 35
- [38] Patient experience in a rare disease: application of the IEXPAC questionnaire in hereditary transthyretin-mediated amyloidosis EXPERT OPINION ON ORPHAN DRUGS, 2021, 9 (06): : 175 - 180