Sustained FVIII Expression with a Tolerable, Titratable, Fully Non-Viral Gene Therapy for Hemophilia a

被引：0
|
作者：
Schwerk, Johannes [1 ]
Barajas-Mora, Mauricio [1 ]
Wang, Hua [1 ]
Truong, Brian [1 ]
Bennett, Michael [1 ]
Cam, Nicholas [1 ]
Clancey, James [1 ]
Davis, Alicia [1 ]
Hajj, Khal [1 ]
Jacques, Bonnie [1 ]
Tamayo, Johnnatan [1 ]
Yen, James [1 ]
Rychak, Joshua [1 ]
Madison, Blair [1 ]
机构：
[1] Poseida Therapeut, San Diego, CA USA
来源：
BLOOD | 2024年 / 144卷
关键词：
D O I：
10.1182/blood-2024-211223
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：7462 / 7463
页数：2
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