Hematopoietic Stem Cell Transplantation Corrects IL-2Rβ Deficiency

被引:0
作者
Alqahtani, Fai [1 ,2 ]
Alghamdi, Manar [2 ]
Alzahrani, Mofareh [3 ]
Alazami, Anas M. [4 ]
Al-Buhairi, Sultan [2 ]
Al-Mousa, Hamoud [2 ,5 ]
机构
[1] Imam Abdulrahman Bin Faisal Univ, King Fahad Hosp Univ, Coll Med, Dept Pediat, Al Khobar, Saudi Arabia
[2] King Faisal Specialist Hosp & Res Ctr, Dept Pediat, Pediat Allergy & Clin Immunol, Riyadh 11211, Saudi Arabia
[3] King Fahad Med City, Dept Pediat, Riyadh, Saudi Arabia
[4] King Faisal Specialist Hosp & Res Ctr, Ctr Genom Med, Translat Genom, Riyadh, Saudi Arabia
[5] Alfaisal Univ, Coll Med, Riyadh, Saudi Arabia
关键词
IL-2R beta; Inborn errors of immunity; Immunodeficiency; Autoimmunity; Hematopoietic stem cell transplantation; Conditioning; SEVERE COMBINED IMMUNODEFICIENCY; EXPRESSION;
D O I
10.1007/s10875-025-01860-8
中图分类号
R392 [医学免疫学]; Q939.91 [免疫学];
学科分类号
100102 ;
摘要
引用
收藏
页数:3
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