Gene therapy for haemophilia clearing house: A single repository of resources for haemophilia

被引:0
作者
O'Mahony, Brian [1 ]
Becker, Tobias [2 ]
Betsch, Carol [3 ]
Buzzi, Andrea [4 ]
Coffin, Donna [5 ]
Grazzi, Enrico Ferri [6 ]
Garcia Diego, Daniel-Anibal [7 ]
Giraud, Nicolas [3 ]
Gomez Cavallini, Antonio [8 ]
Goshen, Dor [9 ]
Hayes, Brendan [10 ]
Page, David [11 ]
Rotellini, Dawn [12 ]
Smith, Clive [13 ]
Liu, Jonathan [14 ]
Njegic, Sanja [15 ]
机构
[1] Irish Haemophilia Soc, Dublin, Ireland
[2] IGH Interessengemein schaft Hamophiler, Rottenburg, Germany
[3] PAG, Assoc Francaise Hemophiles AFH, Paris, France
[4] Fdn Paracelso, Milan, Italy
[5] World Federat Hemophilia, Montreal, PQ, Canada
[6] Fed Emo Federaz Associazioni Emofilici, Milan, Italy
[7] Fedhemo Federac Espanola Hemofilia, Madrid, Spain
[8] Fdn Hemofilia, Buenos Aires, DF, Argentina
[9] Israeli Hemophilia Assoc, Ramat Efal, Israel
[10] Natl Hemophilia Fdn, Plano, TX USA
[11] Canadian Hemophilia Soc, Montreal, PQ, Canada
[12] Natl Bleeding Disorders Fdn, Gibsonia, PA USA
[13] Haemophilia Soc, London, England
[14] BioMarin Pharmaceut Inc, Reading, Berks, England
[15] BioMarin, Basel, Switzerland
关键词
gene therapy; haemophilia; repository;
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
PP-051 (16
引用
收藏
页码:63 / 64
页数:2
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