Accelerating Diverse Cell-Based Therapies Through Scalable Design

被引:2
作者
Peterman, Emma L. [1 ]
Ploessl, Deon S. [1 ]
Galloway, Kate E. [1 ]
机构
[1] MIT, Dept Chem Engn, Cambridge, MA 02139 USA
关键词
cellular engineering; stem cells; biomanufacturing; genome editing; cell-based therapies; synthetic biology; GENE-THERAPY; T-CELLS; DIRECTED DIFFERENTIATION; STEM-CELLS; TRANSGENE EXPRESSION; THYMIDINE KINASE; AAVS1; LOCUS; GENERATION; VECTORS; GENOME;
D O I
10.1146/annurev-chembioeng-100722-121610
中图分类号
O69 [应用化学];
学科分类号
081704 ;
摘要
Augmenting cells with novel, genetically encoded functions will support therapies that expand beyond natural capacity for immune surveillance and tissue regeneration. However, engineering cells at scale with transgenic cargoes remains a challenge in realizing the potential of cell-based therapies. In this review, we introduce a range of applications for engineering primary cells and stem cells for cell-based therapies. We highlight tools and advances that have launched mammalian cell engineering from bioproduction to precision editing of therapeutically relevant cells. Additionally, we examine how transgenesis methods and genetic cargo designs can be tailored for performance. Altogether, we offer a vision for accelerating the translation of innovative cell-based therapies by harnessing diverse cell types, integrating the expanding array of synthetic biology tools, and building cellular tools through advanced genome writing techniques.
引用
收藏
页码:267 / 292
页数:26
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