Cystic fibrosis year in review 2023

被引：1

作者：

Swetland, David V. ^{[1
,2
]}

Savant, Adrienne P. ^{[1
,2
]}

机构：

[1] Childrens Hosp New Orleans, Dept Pediat, New Orleans, LA USA

[2] Tulane Univ, Dept Pediat, New Orleans, LA USA

来源：

PEDIATRIC PULMONOLOGY | 2024年 / 59卷 / 12期

关键词：

CFTR modulators; cystic fibrosis; hepatobiliary; newborn screening; pulmonary exacerbations; LUNG-FUNCTION; PEOPLE; DISEASE;

D O I：

10.1002/ppul.27190

中图分类号：

R72 [儿科学];

学科分类号：

100202 ;

摘要：

This past year, there were many important advances for patients with cystic fibrosis (CF). Of the many publications related to CF in 2023, there was further evaluation of highly effective modulator therapy, new assessments and guidelines for clinical manifestations and therapies for CF, advances in newborn screening and diagnosis, and evaluation of outcomes for people with CF transmembrane conductance regulator-related metabolic syndrome/CF screen positive, inconclusive diagnosis. The aim of this review article is not to provide a full assessment of the wide range of articles published in 2023, but to provide a brief review of publication that may lead to changes in clinical care.

引用

页码：3106 / 3116

页数：11

共 83 条

[1] Lung function decline is mitigated following liver transplantation in people with cystic fibrosis: A retrospective cohort study [J].

Albaiz, Faisal A. ;

Ramos, Kathleen J. ;

Sykes, Jenna ;

Stanojevic, Sanja ;

Ma, Xiayi ;

Quon, Bradley S. ;

Marshall, Bruce C. ;

Cromwell, Elizabeth A. ;

Ostrenga, Joshua S. ;

Faro, Albert ;

Elbert, Alexander ;

Goss, Christopher H. ;

Stephenson, Anne L. .

LIVER TRANSPLANTATION, 2024, 30 (03) :302-310

[2] Cystic fibrosis survival outcomes following second lung transplant: The north American experience [J].

Alshehri, Moayad ;

Ramos, Kathleen J. ;

Sykes, Jenna ;

Ma, Xiayi ;

Stanojevic, Sanja ;

Quon, Bradley S. ;

Marshall, Bruce C. ;

Cromwell, Elizabeth ;

Ostrenga, Joshua S. ;

Faro, Albert ;

Elbert, Alexander ;

Todd, Jonathan ;

Chaparro, Cecilia ;

Goss, Christopher H. ;

Stephenson, Anne L. .

CLINICAL TRANSPLANTATION, 2023, 37 (11)

[3] Suicide attempts in adolescents with cystic fibrosis on Elexacaf tor/Tezacaf tor/Ivacaf tor therapy [J].

Arslan, Meliksah ;

Chalmers, Sarah ;

Rentfrow, Kelly ;

Olson, Janelle M. ;

Dean, Vicki ;

Wylam, Mark E. ;

Demirel, Nadir .

JOURNAL OF CYSTIC FIBROSIS, 2023, 22 (03) :427-430

[4] Positive and negative impacts of elexacaftor/tezacaftor/ivacaftor: Healthcare providers' observations across US centers [J].

Bathgate, Christina J. J. ;

Muther, Emily ;

Georgiopoulos, Anna M. M. ;

Smith, Beth ;

Tillman, Laura ;

Graziano, Sonia ;

Verkleij, Marieke ;

Lomas, Paula ;

Quittner, Alexandra .

PEDIATRIC PULMONOLOGY, 2023, 58 (09) :2469-2477

[5] Adherence, reliability, and variability of home spirometry telemonitoring in cystic fibrosis [J].

Beaufils, Fabien ;

Enaud, Raphael ;

Gallode, Francois ;

Boucher, Gregory ;

Macey, Julie ;

Berger, Patrick ;

Fayon, Michael ;

Bui, Stephanie .

FRONTIERS IN PEDIATRICS, 2023, 11

[6] Impact of elexacaftor/tezacaftor/ivacaftor on bacterial cultures from people with cystic fibrosis [J].

Beck, Michael R. ;

Hornick, Douglas B. ;

Pena, Tahuanty A. ;

Singh, Sachinkumar B. ;

Wright, Brittany A. .

PEDIATRIC PULMONOLOGY, 2023, 58 (05) :1569-1573

[7] Culture result discrepancy between laboratories for nontuberculous mycobacteria in people with cystic fibrosis [J].

Bedoya, Mariana ;

Salfinger, Max ;

Weisman, Alejandra ;

Colin, Andrew A. A. .

PEDIATRIC PULMONOLOGY, 2023, 58 (05) :1598-1601

[8] Home Spirometry in Children with Cystic Fibrosis [J].

Berlinski, Ariel ;

Leisenring, Pamela ;

Willis, Lauren ;

King, Sandra .

BIOENGINEERING-BASEL, 2023, 10 (02)

[9] Factors associated with lung function response with oral antibiotic treatment of pulmonary exacerbations in cystic fibrosis [J].

Blanchard, Ana C. ;

Shaw, Michelle ;

Ratjen, Felix ;

Tullis, Elizabeth ;

Daneman, Nick ;

Waters, Valerie .

JOURNAL OF CYSTIC FIBROSIS, 2023, 22 (05) :880-883

[10] Real-world safety and effectiveness of elexacaf tor/tezacaf tor/ivacaf tor in people with cystic fibrosis: Interim results of a long-term registry-based study [J].

Bower, Julie K. ;

Volkova, Nataliya ;

Ahluwalia, Neil ;

Sahota, Gurvaneet ;

Xuan, Fengjuan ;

Chin, Anna ;

Weinstock, Tanya G. ;

Ostrenga, Josh ;

Elbert, Alexander .

JOURNAL OF CYSTIC FIBROSIS, 2023, 22 (04) :730-737

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