The clinical trials landscape in immunoglobulin light chain amyloidosis: a systematic review

被引:1
作者
Ramachandran, Ramya [1 ]
Shah, Darshi [2 ]
Luo, Catherine [2 ]
Shah, Veer [3 ]
Cliff, Edward R. Scheffer [4 ]
Sanchorawala, Vaishali [5 ,6 ]
Lentzsch, Suzanne [7 ]
Chakraborty, Rajshekhar [7 ]
机构
[1] Hosp Corp Amer Healthcare, Med City Arlington, Arlington, TX USA
[2] SUNY Stony Brook, Renaissance Sch Med, Stony Brook, NY USA
[3] Northeastern Univ, Dept Mech & Ind Engn, Boston, MA USA
[4] Harvard Med Sch, Brigham & Womens Hosp, Div Pharmacoepidemiol & Pharmacoecon, Program Regulat Therapeut & Law, Boston, MA USA
[5] Boston Univ, Dept Med, Amyloidosis Ctr, Chobanian & Avedisian Sch Med, Boston, MA USA
[6] Boston Med Ctr, Boston, MA USA
[7] Columbia Univ, Irving Med Ctr, Dept Med, Multiple Myeloma & Amyloidosis Program, New York, NY USA
关键词
AL AMYLOIDOSIS; OUTCOMES;
D O I
10.1182/bloodadvances.2024012737
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:3464 / 3467
页数:4
相关论文
共 24 条
[1]   Complete responses in AL amyloidosis are unequal the impact of free light chain mass spectrometry in AL [J].
Bomsztyk, Joshua ;
Ravichandran, Sriram ;
V. Giles, Hannah ;
Wright, Nicola ;
Berlanga, Oscar ;
Khwaja, Jahanzaib ;
Mahmood, Shameem ;
Wisniowski, Brendan ;
Cohen, Oliver ;
Foard, Darren ;
Gilbertson, Janet ;
Rauf, Muhammad U. ;
Starr, Neasa ;
Martinez-Naharro, Ana ;
Venneri, Lucia ;
Whelan, Carol ;
Fontana, Marianna ;
Hawkins, Philip N. ;
Gillmore, Julian D. ;
Lachmann, Helen ;
Harding, Stephen ;
Pratt, Guy ;
Wechalekar, Ashutosh D. .
BLOOD, 2024, 143 (13) :1259-1268
[2]   Reduced early mortality with Daratumumab-based frontline therapy in AL amyloidosis: A retrospective cohort study [J].
Chakraborty, Rajshekhar ;
Bhutani, Divaya ;
Mapara, Markus ;
Reshef, Ran ;
Maurer, Mathew S. ;
Radhakrishnan, Jai ;
Lentzsch, Suzanne .
AMERICAN JOURNAL OF HEMATOLOGY, 2024, 99 (03) :477-479
[3]   First report of outcomes in patients with stage IIIb AL amyloidosis treated with Dara-VCD front-line therapy [J].
Chakraborty, Rajshekhar ;
Rosenbaum, Cara ;
Kaur, Gurbakhash ;
Bhutani, Divaya ;
Radhakrishnan, Jai ;
Mapara, Markus Y. ;
Maurer, Mathew ;
Lentzsch, Suzanne .
BRITISH JOURNAL OF HAEMATOLOGY, 2023, 201 (05) :913-916
[4]   Changes in patient-reported outcomes in light chain amyloidosis in the first year after diagnosis and relationship to NT-proBNP change [J].
D'Souza, Anita ;
Brazauskas, Ruta ;
Dispenzieri, Angela ;
Panepinto, Julie ;
Flynn, Kathryn E. .
BLOOD CANCER JOURNAL, 2021, 11 (02)
[5]   The use of PROMIS patient-reported outcomes (PROs) to inform light chain (AL) amyloid disease severity at diagnosis [J].
D'Souza, Anita ;
Magnus, Brooke E. ;
Myers, Judith ;
Dispenzieri, Angela ;
Flynn, Kathryn E. .
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2020, 27 (02) :111-118
[6]   AL amyloidosis patients with low amyloidogenic free light chain levels at first diagnosis have an excellent prognosis [J].
Dittrich, Tobias ;
Bochtler, Tilmann ;
Kimmich, Christoph ;
Becker, Natalia ;
Jauch, Anna ;
Goldschmidt, Hartmut ;
Ho, Anthony D. ;
Hegenbart, Ute ;
Schoenland, Stefan O. .
BLOOD, 2017, 130 (05) :632-642
[7]   Definition of organ involvement and treatment response in immunoglobulin light chain amyloidosis (AL): A consensus opinion from the 10th International Symposium on Amyloid and Amyloidosis [J].
Gertz, MA ;
Comenzo, R ;
Falk, RH ;
Fermand, JP ;
Hazenberg, BP ;
Hawkins, PN ;
Merlini, G ;
Moreau, P ;
Ronco, P ;
Sanchorawala, V ;
Sezer, O ;
Solomon, A ;
Grateau, G .
AMERICAN JOURNAL OF HEMATOLOGY, 2005, 79 (04) :319-328
[8]   Predictors of treatment response and survival outcomes in patients with advanced cardiac AL amyloidosis [J].
Gustine, Joshua N. ;
Staron, Andrew ;
Mendelson, Lisa ;
Joshi, Tracy ;
Gopal, Deepa M. ;
Siddiqi, Omar K. ;
Ruberg, Frederick L. ;
Sanchorawala, Vaishali .
BLOOD ADVANCES, 2023, 7 (20) :6080-6091
[9]   Daratumumab-Based Treatment for Immunoglobulin Light-Chain Amyloidosis [J].
Kastritis, E. ;
Palladini, G. ;
Minnema, M. C. ;
Wechalekar, A. D. ;
Jaccard, A. ;
Lee, H. C. ;
Sanchorawala, V ;
Gibbs, S. ;
Mollee, P. ;
Venner, C. P. ;
Lu, J. ;
Schonland, S. ;
Gatt, M. E. ;
Suzuki, K. ;
Kim, K. ;
Cibeira, M. T. ;
Beksac, M. ;
Libby, E. ;
Valent, J. ;
Hungria, V ;
Wong, S. W. ;
Rosenzweig, M. ;
Bumma, N. ;
Huart, A. ;
Dimopoulos, M. A. ;
Bhutani, D. ;
Waxman, A. J. ;
Goodman, S. A. ;
Zonder, J. A. ;
Lam, S. ;
Song, K. ;
Hansen, T. ;
Manier, S. ;
Roeloffzen, W. ;
Jamroziak, K. ;
Kwok, F. ;
Shimazaki, C. ;
Kim, J-S ;
Crusoe, E. ;
Ahmadi, T. ;
Tran, N. P. ;
Qin, X. ;
Vasey, S. Y. ;
Tromp, B. ;
Schecter, J. M. ;
Weiss, B. M. ;
Zhuang, S. H. ;
Vermeulen, J. ;
Merlini, G. ;
Comenzo, R. L. .
NEW ENGLAND JOURNAL OF MEDICINE, 2021, 385 (01) :46-58
[10]   A prospective observational study of 915 patients with systemic AL amyloidosis treated with upfront bortezomib [J].
Manwani, Richa ;
Cohen, Oliver ;
Sharpley, Faye ;
Mahmood, Shameem ;
Sachchithanantham, Sajitha ;
Foard, Darren ;
Lachmann, Helen J. ;
Quarta, Cristina ;
Fontana, Marianna ;
Gillmore, Julian D. ;
Whelan, Carol ;
Hawkins, Philip N. ;
Wechalekar, Ashutosh D. .
BLOOD, 2019, 134 (25) :2271-2280