Genetic engineering using CRISPR/Cas9 as a strategy for the treatment of Sickle Cell Anemia

被引:0
|
作者
Danda Vasconcelos Santos, M. [1 ]
Nascimento Ferreira, I. [2 ]
Silva Dos Santos, F. [2 ]
Silva Souza, K. [1 ]
Freire Da Silva, M. R. [1 ]
Almeida Candido, M. [1 ]
Motteran, F. [1 ]
Alexandre De Araujo, L. C. [1 ]
Melo De Oliveira, M. B. [1 ]
机构
[1] Fed Univ Pernambuco UFPE, Recife, PE, Brazil
[2] Univ Ctr Sao Francisco River UNIRIOS, Natal, RN, Brazil
关键词
D O I
10.1016/j.cca.2024.118276
中图分类号
R446 [实验室诊断]; R-33 [实验医学、医学实验];
学科分类号
1001 ;
摘要
P0727
引用
收藏
页数:1
相关论文
共 50 条
  • [31] CRISPR/Cas9 System: Use of Genetic Engineering in Healing Cancer and Other Genetic Diseases
    Carvalho, Julia
    Peixoto, Mauricio
    CLINICAL LYMPHOMA MYELOMA & LEUKEMIA, 2022, 22 : S438 - S439
  • [32] Fanconi Anemia Gene Editing by the CRISPR/Cas9 System
    Osborn, Mark J.
    Gabriel, Richard
    Webber, Beau R.
    DeFeo, Anthony P.
    McElroy, Amber N.
    Jarjour, Jordan
    Starker, Colby G.
    Wagner, John E.
    Joung, J. Keith
    Voytas, Daniel F.
    von Kalle, Christof
    Schmidt, Manfred
    Blazar, Bruce R.
    Tolar, Jakub
    HUMAN GENE THERAPY, 2015, 26 (02) : 114 - 126
  • [33] The Potential of CRISPR/Cas9 Gene Editing as a Treatment Strategy for Inherited Diseases
    Abdelnour, Sameh A.
    Xie, Long
    Hassanin, Abdallah A.
    Zuo, Erwei
    Lu, Yangqing
    FRONTIERS IN CELL AND DEVELOPMENTAL BIOLOGY, 2021, 9
  • [34] Efficient CRISPR/Cas9 genome engineering using zygotes and embryos derived from transgenic mice overexpressing Cas9
    Cebrian-Serrano, Alberto
    Preece, Chris
    Biggs, Daniel
    Davies, Benjamin
    TRANSGENIC RESEARCH, 2016, 25 (02) : 225 - 225
  • [35] Genome Engineering of Primary Human B Cells Using CRISPR/Cas9
    Laoharawee, Kanut
    Johnson, Matthew J.
    Lahr, Walker S.
    Peterson, Joseph J.
    Webber, Beau R.
    Moriarity, Branden S.
    JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, 2020, (165):
  • [36] Genetic engineering to enhance microalgal-based produced water treatment with emphasis on CRISPR/Cas9: A review
    Hassanien, Alaa
    Saadaoui, Imen
    Schipper, Kira
    Al-Marri, Sara
    Dalgamouni, Tasneem
    Aouida, Mustapha
    Saeed, Suhur
    Al-Jabri, Hareb M. M.
    FRONTIERS IN BIOENGINEERING AND BIOTECHNOLOGY, 2023, 10
  • [37] Engineering Plant Immunity: Using CRISPR/Cas9 to Generate Virus Resistance
    Zaidi, Syed Shan-e-Ali
    Tashkandi, Menai
    Mansoor, Shahid
    Mahfouz, Magdy M.
    FRONTIERS IN PLANT SCIENCE, 2016, 7
  • [38] Engineering novel human sweat gland cell lines using CRISPR/Cas9 and primary cell technologies
    Wursthorn, A.
    Sturmheit, T.
    Pul, U.
    Kier, J.
    Brandenburger, M.
    Ertongur-Fauth, T.
    JOURNAL OF INVESTIGATIVE DERMATOLOGY, 2017, 137 (10) : S235 - S235
  • [39] Multiplex metabolic pathway engineering using CRISPR/Cas9 in Saccharomyces cerevisiae
    Jakounas, Tadas
    Sonde, Ida
    Herrgard, Markus
    Harrison, Scott J.
    Kristensen, Mette
    Pedersen, Lasse E.
    Jensen, Michael K.
    Keasling, Jay D.
    METABOLIC ENGINEERING, 2015, 28 : 213 - 222
  • [40] Reverse-engineering the serrated neoplasia pathway using CRISPR–Cas9
    Arne Bleijenberg
    Evelien Dekker
    Nature Reviews Gastroenterology & Hepatology, 2018, 15 (9) : 522 - 524