Genetic engineering using CRISPR/Cas9 as a strategy for the treatment of Sickle Cell Anemia

被引:0
|
作者
Danda Vasconcelos Santos, M. [1 ]
Nascimento Ferreira, I. [2 ]
Silva Dos Santos, F. [2 ]
Silva Souza, K. [1 ]
Freire Da Silva, M. R. [1 ]
Almeida Candido, M. [1 ]
Motteran, F. [1 ]
Alexandre De Araujo, L. C. [1 ]
Melo De Oliveira, M. B. [1 ]
机构
[1] Fed Univ Pernambuco UFPE, Recife, PE, Brazil
[2] Univ Ctr Sao Francisco River UNIRIOS, Natal, RN, Brazil
关键词
D O I
10.1016/j.cca.2024.118276
中图分类号
R446 [实验室诊断]; R-33 [实验医学、医学实验];
学科分类号
1001 ;
摘要
P0727
引用
收藏
页数:1
相关论文
共 50 条
  • [1] Heritable Multiplex Genetic Engineering in Rats Using CRISPR/Cas9
    Ma, Yuanwu
    Shen, Bin
    Zhang, Xu
    Lu, Yingdong
    Chen, Wei
    Ma, Jing
    Huang, Xingxu
    Zhang, Lianfeng
    PLOS ONE, 2014, 9 (03):
  • [2] Engineering of actinomycetes using CRISPR/Cas9 technologies
    Weber, T.
    Tong, Y.
    Blin, K.
    Lee, S. Y.
    PLANTA MEDICA, 2016, 82
  • [3] CRISPR/Cas9 gene editing for curing sickle cell disease
    Park, So Hyun
    Bao, Gang
    TRANSFUSION AND APHERESIS SCIENCE, 2021, 60 (01)
  • [4] CRISPR/Cas9 advances engineering of microbial cell factories
    Jakociunas, Tadas
    Jensen, Michael K.
    Keasling, Jay D.
    METABOLIC ENGINEERING, 2016, 34 : 44 - 59
  • [5] CRISPR/Cas9 Targeted Gene Editing and Cellular Engineering in Fanconi Anemia
    Osborn, Mark J.
    Lonetree, Cara-Lin
    Webber, Beau R.
    Patel, Dharmeshkumar
    Dunmire, Samantha
    DeFeo, Anthony P.
    McElroy, Amber N.
    MacMillan, Margaret L.
    Wagner, John E.
    Blazar, Bruce R.
    Tolar, Jakub
    STEM CELLS AND DEVELOPMENT, 2016, 25 (20) : 1591 - 1603
  • [6] Engineering Citrobacter freundii using CRISPR/Cas9 system
    Alfaro, Trinidad
    Elmore, Joshua R.
    Stromberg, Zachary R.
    Hutchison, Janine R.
    Hess, Becky M.
    JOURNAL OF MICROBIOLOGICAL METHODS, 2022, 200
  • [7] Engineering the mouse genome using CRISPR/Cas9 technology
    Mianne, Joffrey
    Caulder, Adam
    Codner, Gemma
    King, Ruairidh
    Fell, Rachel
    Maritati, Marina
    Allan, Alasdair
    Jarrold, James
    Fray, Martin
    Gardiner, Wendy
    Wells, Sara
    Teboul, Lydia
    TRANSGENIC RESEARCH, 2016, 25 (02) : 251 - 251
  • [8] Chromosome engineering in zygotes with CRISPR/Cas9
    Boroviak, Katharina
    Doe, Brendan
    Banerjee, Ruby
    Yang, Fengtang
    Bradley, Allan
    GENESIS, 2016, 54 (02) : 78 - 85
  • [9] Correction of Fanconi Anemia Mutation Using the Crispr/Cas9 System
    Kawashima, Nozomu
    Okuno, Yusuke
    Sekiya, Yuko
    Wang, Xinan
    Narita, Atsushi
    Doisaki, Sayoko
    Kamei, Michi
    Nishio, Nobuhiro
    Muramatsu, Hideki
    Hama, Asahito
    Takahashi, Yoshiyuki
    Kojima, Seiji
    BLOOD, 2015, 126 (23)
  • [10] Improving the efficiency of Cas9/CRISPR genome engineering by optimizing Cas9 delivery
    Pelczar, Pawel
    Oller, Heide
    Kornete, Mara
    Schreiner, Dietmar
    Hermann, Mario
    Jeker, Lukas
    TRANSGENIC RESEARCH, 2016, 25 (02) : 255 - 256