Orchard Therapeutics Gains First US Approval for a Metachromatic Leukodystrophy Gene Therapy

被引：6

作者：

Philippidis, Alex ^{[1
]}

机构：

[1] Mary Ann Liebert Inc, New Rochelle, NY 10801 USA

来源：

HUMAN GENE THERAPY | 2024年 / 35卷 / 7-8期

关键词：

D O I：

10.1089/hum.2024.29268.bfs

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

[No abstract available]

引用

页码：215 / 218

页数：4

共 50 条

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