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- [1] Gene Therapy with Fidanacogene Elaparvovec in Adults with Hemophilia BNEW ENGLAND JOURNAL OF MEDICINE, 2024, 391 (12): : 1108 - 1118Cuker, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAKavakli, K.论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Fac Med, Dept Pediat, Div Hematol, Izmir, Turkiye Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAFrenzel, L.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Inst Imagine, Dept Hematol Hemophilia Care & Res, Paris, France Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAWang, J-D论文数: 0 引用数: 0 h-index: 0机构: Taichung Vet Gen Hosp, Ctr Rare Dis & Hemophilia, Taichung, Taiwan Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAAstermark, J.论文数: 0 引用数: 0 h-index: 0机构: Lund Univ, Dept Translat Med, Lund, Sweden Skane Univ Hosp, Dept Hematol Oncol & Radiat Phys, Malmo, Sweden Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USACerqueira, M. H.论文数: 0 引用数: 0 h-index: 0机构: Inst Hematol Estado Rio de Janeiro, Rio De Janeiro, Brazil Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAIorio, A.论文数: 0 引用数: 0 h-index: 0机构: McMaster Univ, Dept Hlth Res Methods Evidence & Impact, Hamilton, ON, Canada McMaster Univ, Dept Med, Hamilton, ON, Canada Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAKatsarou-Fasouli, O.论文数: 0 引用数: 0 h-index: 0机构: Laikon Gen Hosp, Blood Transfus Ctr, Natl Reference Ctr Congenital Bleeding Disorders, Athens, Greece Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAKlamroth, R.论文数: 0 引用数: 0 h-index: 0机构: Vivantes Hosp Friedrichshain, Berlin, Germany Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAShapiro, A. D.论文数: 0 引用数: 0 h-index: 0机构: Indiana Hemophilia & Thrombosis Ctr, Indianapolis, IN USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAHermans, C.论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, Div Hematol, Hemostasis & Thrombosis Unit, Clin Univ St Luc, Brussels, Belgium Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAIshiguro, A.论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Child Hlth & Dev, Div Hematol, Tokyo, Japan Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USALeavitt, A. D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Dept Med, San Francisco, CA 94143 USA Univ Calif San Francisco, Dept Lab Med, San Francisco, CA USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAOldenburg, J. B.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Bonn, Inst Expt Hematol & Transfus Med, Bonn, Germany Univ Clin Bonn, Ctr Rare Dis Bonn, Bonn, Germany Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAOzelo, M. C.论文数: 0 引用数: 0 h-index: 0机构: Univ Estadual Campinas, Hemoctr UNICAMP, Sch Med Sci, Dept Internal Med, Campinas, Brazil Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USATeitel, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Div Hematol, St Michaels Hosp, Toronto, ON, Canada Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USABiondo, F.论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Rome, Italy Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAFang, A.论文数: 0 引用数: 0 h-index: 0机构: Pfizer, New York, NY USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAFuiman, J.论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Collegeville, PA USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USAMcKay, J.论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Groton, CT USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USASun, P.论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Cambridge, MA USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USARasko, J. E. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Fac Med & Hlth, Cent Clin Sch, Sydney, NSW, Australia Univ Sydney, Gene & Stem Cell Therapy Program, Centenary Inst, Sydney, NSW, Australia Royal Prince Alfred Hosp, Dept Cell & Mol Therapies, Sydney, NSW, Australia Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USARupon, J.论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Collegeville, PA USA Univ Penn, Perelman Sch Med, Dept Med, Philadelphia, PA 19104 USA
- [2] Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia BNEW ENGLAND JOURNAL OF MEDICINE, 2014, 371 (21): : 1994 - 2004Nathwani, A. C.论文数: 0 引用数: 0 h-index: 0机构: Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England Royal Free NHS Trust, Thrombosis Unit, London, England UCL, Inst Canc, Dept Haematol, London, England NHS Blood & Transplant, Watford, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandReiss, U. M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandTuddenham, E. G. D.论文数: 0 引用数: 0 h-index: 0机构: Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England Royal Free NHS Trust, Thrombosis Unit, London, England UCL, Inst Canc, Dept Haematol, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandRosales, C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Canc, Dept Haematol, London, England NHS Blood & Transplant, Watford, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandChowdary, P.论文数: 0 引用数: 0 h-index: 0机构: Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England Royal Free NHS Trust, Thrombosis Unit, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandMcIntosh, J.论文数: 0 引用数: 0 h-index: 0机构: Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England Royal Free NHS Trust, Thrombosis Unit, London, England UCL, Inst Canc, Dept Haematol, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandDella Peruta, M.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Canc, Dept Haematol, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandLheriteau, E.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Canc, Dept Haematol, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandPatel, N.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Canc, Dept Haematol, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandRaj, D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Canc, Dept Haematol, London, England NHS Blood & Transplant, Watford, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandRiddell, A.论文数: 0 引用数: 0 h-index: 0机构: Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England Royal Free NHS Trust, Thrombosis Unit, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandPie, J.论文数: 0 引用数: 0 h-index: 0机构: Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England Royal Free NHS Trust, Thrombosis Unit, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandRangarajan, S.论文数: 0 引用数: 0 h-index: 0机构: St Thomas Hosp, London, England Basingstoke & North Hampshire Fdn Trust, Basingstoke, Hants, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandBevan, D.论文数: 0 引用数: 0 h-index: 0机构: St Thomas Hosp, London, England Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England论文数: 引用数: h-index:机构:Shen, Y. -M.论文数: 0 引用数: 0 h-index: 0机构: Univ Texas SW Med Ctr Dallas, Dept Internal Med, Dallas, TX 75390 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandHalka, K. G.论文数: 0 引用数: 0 h-index: 0机构: Scott & White Healthcare, Temple Clin, Temple, TX USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandBasner-Tschakarjan, E.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandMingozzi, F.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandHigh, K. A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandAllay, J.论文数: 0 引用数: 0 h-index: 0机构: Poplar Healthcare, Memphis, TN USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandKay, M. A.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Dept Pediat, Palo Alto, CA 94304 USA Stanford Univ, Sch Med, Dept Genet, Palo Alto, CA 94304 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandNg, C. Y. C.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Surg, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandZhou, J.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Surg, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandCancio, M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Surg, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandMorton, C. L.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Surg, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandGray, J. T.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandSrivastava, D.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Biostat, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandNienhuis, A. W.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, EnglandDavidoff, A. M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Surg, Memphis, TN 38105 USA Royal Free NHS Trust, Katharine Dormandy Haemophilia Ctr, London, England
- [3] Comprehensive analysis and prediction of long-term durability of factor IX activity following etranacogene dezaparvovec gene therapy in the treatment of hemophilia BCURRENT MEDICAL RESEARCH AND OPINION, 2023, 39 (02) : 227 - 237Shah, Jinesh论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USAKim, Hongseok论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USASivamurthy, Krupa论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USAMonahan, Paul E.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USAFries, Michael论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, King Of Prussia, PA USA
- [4] Efficacy and Safety in 15 Hemophilia B Patients Treated with the AAV Gene Therapy Vector Fidanacogene Elaparvovec and Followed for at Least 1 YearBLOOD, 2019, 134George, Lindsey A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USASullivan, Spencer K.论文数: 0 引用数: 0 h-index: 0机构: Mississippi Ctr Adv Med, Madison, MS USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USARasko, John E. J.论文数: 0 引用数: 0 h-index: 0机构: Centenary Inst, Gene & Stem Cell Therapy Program, Camperdown, NSW, Australia Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USAGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA 95817 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USASamelson-Jones, Benjamin J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USADucore, Jonathan M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USATeitel, Jerome M.论文数: 0 引用数: 0 h-index: 0机构: St Michaels Hosp, Div Hematol & Oncol, Dept Med, Toronto, ON, Canada Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USAMcGuinn, Catherine E.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, New York, NY USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USARunowski, Alexa R.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USAWright, Fraser论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Ctr Definit & Curat Med, Stanford, CA 94305 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USAAnguela, Xavier M.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut, Philadelphia, PA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USAHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut, Philadelphia, PA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USARybin, Denis论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Cambridge, MA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USAMurphy, John E.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Corp, Rare Dis Res Unit, Cambridge, MA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USARupon, Jeremy论文数: 0 引用数: 0 h-index: 0机构: Pfizer, Collegeville, PA USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
- [5] PATTERNS OF JOINT BLEEDS IN PATIENTS WITH HEMOPHILIA B FOLLOWING FIDANACOGENE ELAPARVOVEC ADENO-ASSOCIATED VIRUS GENE THERAPYHAEMOPHILIA, 2023, 29 : 113 - 114Rasko, J. E. J.论文数: 0 引用数: 0 h-index: 0机构: Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, Australia Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaChhabra, A.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaDucore, J. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaGeorge, L. A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Philadelphia, PA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaGiermasz, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaHigh, K.论文数: 0 引用数: 0 h-index: 0机构: Spark Therapeut, Philadelphia, PA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaMcGuinn, C. E.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, New York, NY USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaO'Brien, A.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaRupon, J.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaSamelson-Jones, B. J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Philadelphia, PA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaSmith, L. M.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaSullivan, S. K.论文数: 0 引用数: 0 h-index: 0机构: Mississippi Ctr Adv, Madison, MS USA Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaTeitel, J. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, St Michaels Hosp, Toronto, ON, Canada Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, AustraliaWinburn, I.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Ltd, Tadworth, England Royal Prince Alfred Hosp, SLHD, Cell & Mol Therapies, Camperdown, Australia
- [6] Characterizing a Cohort of Patients with Hemophilia B Treated with Fidanacogene Elaparvovec from the Phase 3 Benegene-2 Study Who Returned to Factor IX ProphylaxisBLOOD, 2023, 142Frenzel, Laurent论文数: 0 引用数: 0 h-index: 0机构: Inst Necker, Dept Haematol, Paris, France Inst Necker, Dept Haematol, Paris, FranceKavakli, Kaan论文数: 0 引用数: 0 h-index: 0机构: Ege Univ, Fac Med, Dept Pediat, Div Hematol, Izmir, Turkiye Inst Necker, Dept Haematol, Paris, FranceKlamroth, Robert论文数: 0 引用数: 0 h-index: 0机构: Vivantes Clin Friedrichshain, Internal Med Vasc Med & Coagulat Disorders, Berlin, Germany Inst Necker, Dept Haematol, Paris, FranceChiou, Shyh-Shin论文数: 0 引用数: 0 h-index: 0机构: Kaohsiung Med Univ, Div Pediat Hematol & Oncol, Dept Pediat, Kaohsiung, Taiwan Inst Necker, Dept Haematol, Paris, FranceShapiro, Amy D.论文数: 0 引用数: 0 h-index: 0机构: Indiana Hemophilia & Thrombosis Ctr Inc, Indianapolis, IN USA Inst Necker, Dept Haematol, Paris, FranceSun, Pengling论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Cambridge, MA USA Inst Necker, Dept Haematol, Paris, FranceFuiman, Joanne论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Inst Necker, Dept Haematol, Paris, FranceMcKay, John论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Groton, CT 06340 USA Inst Necker, Dept Haematol, Paris, FranceFang, Annie F.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Inst Necker, Dept Haematol, Paris, FranceBiondo, Francesca论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Groton, CT 06340 USA Inst Necker, Dept Haematol, Paris, FrancePlonski, Frank论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Inst Necker, Dept Haematol, Paris, FranceRupon, Jeremy论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Inst Necker, Dept Haematol, Paris, France
- [7] A MULTI-YEAR FOLLOW-UP STUDY OF FIDANACOGENE ELAPARVOVEC GENE THERAPY FOR HEMOPHILIA BAMERICAN JOURNAL OF HEMATOLOGY, 2024, 100 : 112 - 112Samelson-Jones, Benjamin J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAGeorge, Lindsey A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USARasko, John E. J.论文数: 0 引用数: 0 h-index: 0机构: Royal Prince Alfred Hosp, Dept Cell & Mol Therapies, Sydney, NSW, Australia Univ Sydney, Centenary Inst, Fac Med & Hlth, Gene & Stem Cell Therapy Program, Sydney, NSW, Australia Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA 95817 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USATeitel, Jerome M.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, St Michaels Hosp, Toronto, ON, Canada Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAMcGuinn, Catherine E.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med, New York, NY USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USADucore, Jonathan M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA 95817 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAPennington, Sharon论文数: 0 引用数: 0 h-index: 0机构: Mississippi Ctr Adv Med, Madison, MS USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAHigh, Katherine A.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USARupon, Jeremy论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USABiondo, Francesca论文数: 0 引用数: 0 h-index: 0机构: Pfizer Srl, Rome, Italy Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAFang, Annie论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USASmith, Lynne M.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAKalac, Matko论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAChhabra, Amit论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAPlonski, Frank论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
- [8] Health-Related Quality of Life in Adults with Hemophilia B after Receiving Gene Therapy with Fidanacogene ElaparvovecBLOOD, 2023, 142von Mackensen, Sylvia论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, Germany Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyDucore, Jonathan M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyGeorge, Lindsey A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA 95817 USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyMcGuinn, Catherine论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Pediat Hematol Oncol Div, New York, NY USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyRasko, John E. J.论文数: 0 引用数: 0 h-index: 0机构: Royal Prince Alfred Hosp, Dept Cell & Mol Therapies, Sydney, NSW, Australia Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanySamelson-Jones, Ben J.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Dept Pediat, Philadelphia, PA 19104 USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanySullivan, Spencer K.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyTeitel, Jerome M.论文数: 0 引用数: 0 h-index: 0机构: St Michaels Hosp, Toronto, ON, Canada Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyChhabra, Amit论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyFang, Annie F.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyO'Brien, Amanda论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyPlonski, Frank论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyRupon, Jeremy论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanySmith, Lynne论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, GermanyWinburn, Ian论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Tadworth, England Univ Med Ctr Hamburg Eppendorf, Dept Med Psychol, Hamburg, Germany
- [9] Follow-up of More Than 5 Years in a Cohort of Patients with Hemophilia B Treated with Fidanacogene Elaparvovec Adeno-Associated Virus Gene TherapyBLOOD, 2021, 138Samelson-Jones, Ben J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA USA Childrens Hosp Philadelphia, Philadelphia, PA USASullivan, Spencer K.论文数: 0 引用数: 0 h-index: 0机构: Mississippi Ctr Adv Med, Madison, MS USA Childrens Hosp Philadelphia, Philadelphia, PA USARasko, John E. J.论文数: 0 引用数: 0 h-index: 0机构: Royal Prince Alfred Hosp, Cell Mol Therapies, Camperdown, NSW, Australia Childrens Hosp Philadelphia, Philadelphia, PA USAGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Sacramento, CA USA Childrens Hosp Philadelphia, Philadelphia, PA USAGeorge, Lindsey A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA USA Univ Pennsylvania, Perelman Sch Med, Philadelphia, PA USA Childrens Hosp Philadelphia, Philadelphia, PA USADucore, Jonathan M.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA USA Childrens Hosp Philadelphia, Philadelphia, PA USATeitel, Jerome M.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, St Michaels Hosp, Toronto, ON, Canada Childrens Hosp Philadelphia, Philadelphia, PA USAMcGuinn, Catherine E.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, New York, NY USA Childrens Hosp Philadelphia, Philadelphia, PA USAO'Brien, Amanda论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Childrens Hosp Philadelphia, Philadelphia, PA USAWinburn, Ian论文数: 0 引用数: 0 h-index: 0机构: Pfizer Ltd, Surrey, England Childrens Hosp Philadelphia, Philadelphia, PA USASmith, Lynne M.论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Childrens Hosp Philadelphia, Philadelphia, PA USAChhabra, Amit论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, New York, NY USA Childrens Hosp Philadelphia, Philadelphia, PA USARupon, Jeremy论文数: 0 引用数: 0 h-index: 0机构: Pfizer Inc, Collegeville, PA USA Childrens Hosp Philadelphia, Philadelphia, PA USA
- [10] Gene therapy for patients with hemophilia B is superior to factor IX administrationDEUTSCHE MEDIZINISCHE WOCHENSCHRIFT, 2023, 148 (23) : 1488 - 1488Franke, Katharina论文数: 0 引用数: 0 h-index: 0