Generation of Alzheimer's Disease Model Derived from Induced Pluripotent Stem Cells with APP Gene Mutation

被引:1
作者
Kim, Yena [1 ,2 ]
Yun, Binna [1 ,2 ]
Ye, Byoung Seok [3 ]
Kim, Bo-Young [1 ,2 ]
机构
[1] Korea Natl Inst Hlth, Dept Chron Dis Convergence Res, Div Intractable Dis Res, Cheongju 28160, South Korea
[2] Korea Natl Inst Hlth, Natl Stem Cell Bank Korea, Cheongju 28160, South Korea
[3] Yonsei Univ, Coll Med, Dept Neurol, Seoul 03722, South Korea
关键词
Alzheimer's disease; amyloid precursor protein; cerebral organoid; disease modeling; drug screening; induced pluripotent stem cells; organoids; tau pathology; TAU; CHALLENGES;
D O I
10.3390/biomedicines12061193
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
Alzheimer's disease (AD), the most common cause of dementia, is characterized by disruptions in memory, cognition, and personality, significantly impacting morbidity and mortality rates among older adults. However, the exact pathophysiological mechanism of AD remains unknown, and effective treatment options for AD are still lacking. Human induced pluripotent stem cells (iPSC) are emerging as promising platforms for disease research, offering the ability to model the genetic mutations associated with various conditions. Patient-derived iPSCs are useful for modeling neurodegenerative and neurodevelopmental disorders. In this study, we generated AD iPSCs from peripheral blood mononuclear cells obtained from a 65-year-old patient with AD carrying the E682K mutation in the gene encoding the amyloid precursor protein. Cerebral organoids derived from AD iPSCs recapitulated the AD phenotype, exhibiting significantly increased levels of tau protein. Our analysis revealed that an iPSC disease model of AD is a valuable assessment tool for pathophysiological research and drug screening.
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页数:11
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