Spinal Muscular Atrophy: Expanded Access as an Instrument of Fairness

被引:0
|
作者
Beninger, Paul [1 ]
机构
[1] Tufts Univ, Sch Med, Publ Hlth & Community Med, Boston, MA 02155 USA
关键词
D O I
10.1016/j.clinthera.2024.03.010
中图分类号
R9 [药学];
学科分类号
1007 ;
摘要
引用
收藏
页码:305 / 306
页数:2
相关论文
共 50 条
  • [41] Understanding spinal muscular atrophy
    不详
    Nature Structural Biology, 2001, 8 (1) : 1 - 1
  • [42] Bone and Spinal Muscular Atrophy
    Vai, Silvia
    Bianchi, Maria Luisa
    Moroni, Isabella
    Mastella, Chiara
    Broggi, Francesca
    Morandi, Lucia
    Arnoldi, Maria Teresa
    Bussolino, Chiara
    Baranello, Giovanni
    BONE, 2015, 79 : 116 - 120
  • [43] Nusinersen for spinal muscular atrophy
    Wurster, Claudia D.
    Ludolph, Albert C.
    THERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS, 2018, 11
  • [44] Spinal muscular atrophy diagnostics
    Prior, Thomas W.
    JOURNAL OF CHILD NEUROLOGY, 2007, 22 (08) : 952 - 956
  • [45] Issue of spinal muscular Atrophy
    Boukis, Costas
    MONATSSCHRIFT FUR PSYCHIATRIE UND NEUROLOGIE, 1937, 96 (1-2): : 1 - 12
  • [46] PROXIMAL SPINAL MUSCULAR ATROPHY
    ZELLWEGER, H
    HANHART, E
    FRANK, A
    NEUROPADIATRIE, 1972, 3 (04): : 327 - +
  • [47] Fractures in spinal muscular atrophy
    Febrer, Anna
    Vigo, Meritxell
    Rodriguez, Natalia
    Medina, Julita
    Colomer, Jaume
    Nascimento, Andres
    REVISTA DE NEUROLOGIA, 2013, 57 (05) : 207 - 211
  • [48] Hydroxyurea for spinal muscular atrophy
    不详
    PROGRESS IN NEUROLOGY AND PSYCHIATRY, 2011, 15 (01) : 35 - 35
  • [49] SPINAL MUSCULAR-ATROPHY
    WESSEL, HB
    PEDIATRIC ANNALS, 1989, 18 (07): : 421 - &
  • [50] Screening for spinal muscular atrophy
    Sampaio, Hugo
    Wilcken, Bridget
    Farrar, Michelle
    MEDICAL JOURNAL OF AUSTRALIA, 2018, 209 (04) : 147 - +