Lumasiran for Patients With Primary Hyperoxaluria Type 1 and Impaired Kidney Function: 12-Month Analysis of the Phase 3 ILLUMINATE-C Trial

被引:0
作者
Frishberg, Yaacov [1 ]
Michael, Mini [2 ,3 ]
Groothoff, Jaap [4 ,5 ]
Shasha-Lavsky, Hadas [6 ]
Lieske, John C. [7 ]
Simkova, Eva [8 ]
Sellier-Leclerc, Anne-Laure A. [9 ]
Devresse, Arnaud [10 ]
Egziabher, Fitsum Guebre [11 ]
Bakkaloglu, Sevcan A. [12 ]
Mourani, Chebl [17 ]
Saqan, Rola [13 ]
Singer, Richard F. [14 ]
Willey, Richard G. [15 ]
Gansner, John M. [15 ]
Magen, Daniella [16 ]
机构
[1] Shaare Zedek Med Ctr, Jerusalem, Israel
[2] Texas Childrens Hosp, Houston, TX USA
[3] Baylor Coll Med, Houston, TX USA
[4] Emmas Childrens Hosp, Amsterdam, Netherlands
[5] Univ Amsterdam, Dept Pediat Nephrol, Amsterdam, Netherlands
[6] Galilee Med Ctr, Nahariyya, Israel
[7] Mayo Clin, Div Nephrol & Hypertens, Rochester, MN USA
[8] Al Jalila Childrens Specialty Hosp, Dubai, U Arab Emirates
[9] Hop Femme Mere Enfant, Bron, France
[10] Clin Univ St Luc, Brussels, Belgium
[11] Hop Edouard Herriot, Lyon, France
[12] Gazi Univ, Ankara, Turkiye
[13] Jordan Univ Sci & Technol, Irbid, Jordan
[14] Canberra Hlth Serv, Garran, ACT, Australia
[15] Alnylam Pharmaceut Inc, Cambridge, MA USA
[16] Rambam Hlth Care Campus, Haifa, Israel
[17] Hotel Dieu France, Beirut, Lebanon
来源
JOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY | 2022年 / 33卷 / 11期
关键词
D O I
暂无
中图分类号
R5 [内科学]; R69 [泌尿科学(泌尿生殖系疾病)];
学科分类号
1002 ; 100201 ;
摘要
FR-PO335
引用
收藏
页码:416 / 416
页数:1
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