Volanesorsen and triglyceride levels in familial chylomicronemia syndrome: Long-term efficacy and safety data from patients in an open-label extension trial (vol 17, pg 342, 2023)

被引：0

作者：

Witztum, Joseph L. ^{[1
]}

Gaudet, Daniel ^{[2
,3
]}

Arca, Marcello ^{[4
]}

Jones, Alan ^{[5
]}

Soran, Handrean ^{[6
]}

Gouni-Berthold, Ioanna ^{[7
,8
]}

Stroes, Erik S. G. ^{[9
]}

Alexander, Veronica J. ^{[10
]}

Jones, Richard ^{[11
]}

Watts, Lynnetta ^{[10
]}

Xia, Shuting ^{[10
]}

Tsimikas, Sotirios ^{[1
,10
]}

机构：

[1] Univ Calif San Diego, Dept Med, Room 1081,9500 Gilman Dr, La Jolla, CA 92093 USA

[2] Univ Montreal, Community Genom Med Ctr, Dept Med, Lipidol Unit, 930 Jacques Cartier Est, Chicoutimi, PQ G7H 7K9, Canada

[3] ECOGENE 21, 930 Jacques Cartier Est, Chicoutimi, PQ G7H 7K9, Canada

[4] Univ Roma La Sapienza, Dept Translat & Precis Med, Viale Univ 37, I-00185 Rome, Italy

[5] Univ Hosp Birmingham NHS Fdn Trust, Heartlands Hosp, Bordesley Green E, Birmingham B9 5SS, England

[6] Manchester Univ NHS Fdn Trust, Manchester Royal Infirm, Oxford Rd, Manchester M13 9WL, England

[7] Univ Cologne, Fac Med, Ctr Endocrinol Diabet & Prevent Med, Kerpener Str 62, D-50937 Cologne, Germany

[8] Univ Hosp Cologne, Kerpener Str 62, D-50937 Cologne, Germany

[9] Acad Med Ctr, Dept Vasc Med, Meibergdreef 9, NL-1105 AZ Amsterdam, Netherlands

[10] Ionis Pharmaceut, 2855 Gazelle Court, Carlsbad, CA 92010 USA

[11] Akcea Therapeut, St James House,72 Adelaide Rd 2, Dublin D02 Y017, Ireland

来源：

JOURNAL OF CLINICAL LIPIDOLOGY | 2024年 / 18卷 / 03期

关键词：

D O I：

10.1016/j.jacl.2023.09.010

中图分类号：

R9 [药学];

学科分类号：

1007 ;

摘要：

引用

页码：e482 / e483

页数：2

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