Seven-year follow-up of valoctocogene roxaparvovec gene therapy for haemophilia A

被引:0
作者
Symington, E. [1 ]
Rangarajan, S. [2 ]
Lester, W. [3 ]
Madan, B. [4 ]
Pierce, G. F.
Raheja, P. [5 ]
Millar, C. [6 ,7 ]
Osmond, D. [8 ]
Li, M. [8 ]
Robinson, T. M. [8 ]
机构
[1] Cambridge Univ Hosp NHS Fdn Trust, Cambridge, England
[2] Univ Southampton, Fac Med, Southampton, Hants, England
[3] Univ Hosp Birmingham NHS Fdn Trust, Birmingham, W Midlands, England
[4] Guys & St Thomas NHS Fdn Trust, London, England
[5] Barts Hlth NHS Trust, Haemophilia Ctr, Royal London Hosp, London, England
[6] Imperial Coll Healthcare NHS Trust, London, England
[7] Imperial Coll London, Ctr Haematol, Dept Immunol & Inflammat, London, England
[8] BioMarin Pharmaceut Inc, Novato, CA USA
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D O I
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中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
PO124
引用
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页码:96 / 97
页数:2
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