CYSTIC-FIBROSIS - VEHICLES FOR GENE-THERAPY

被引:53
作者
WILSON, JM
机构
关键词
D O I
10.1038/365691a0
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
引用
收藏
页码:691 / 692
页数:2
相关论文
共 10 条
  • [1] NONINVASIVE LIPOSOME-MEDIATED GENE DELIVERY CAN CORRECT THE ION-TRANSPORT DEFECT IN CYSTIC-FIBROSIS MUTANT MICE
    ALTON, EWFW
    MIDDLETON, PG
    CAPLEN, NJ
    SMITH, SN
    STEEL, DM
    MUNKONGE, FM
    JEFFERY, PK
    GEDDES, DM
    HART, SL
    WILLIAMSON, R
    FASOLD, KI
    MILLER, AD
    DICKINSON, P
    STEVENSON, BJ
    MCLACHLAN, G
    DORIN, JR
    PORTEOUS, DJ
    [J]. NATURE GENETICS, 1993, 5 (02) : 135 - 142
  • [2] DEFECTIVE EPITHELIAL CHLORIDE TRANSPORT IN A GENE-TARGETED MOUSE MODEL OF CYSTIC-FIBROSIS
    CLARKE, LL
    GRUBB, BR
    GABRIEL, SE
    SMITHIES, O
    KOLLER, BH
    BOUCHER, RC
    [J]. SCIENCE, 1992, 257 (5073) : 1125 - 1128
  • [3] ENGELHARDT JE, IN PRESS J CLIN INVE
  • [4] SUBMUCOSAL GLANDS ARE THE PREDOMINANT SITE OF CFTR EXPRESSION IN THE HUMAN BRONCHUS
    ENGELHARDT, JF
    YANKASKAS, JR
    ERNST, SA
    YANG, YP
    MARINO, CR
    BOUCHER, RC
    COHN, JA
    WILSON, JM
    [J]. NATURE GENETICS, 1992, 2 (03) : 240 - 248
  • [5] CORRECTION OF THE ION-TRANSPORT DEFECT IN CYSTIC-FIBROSIS TRANSGENIC MICE BY GENE-THERAPY
    HYDE, SC
    GILL, DR
    HIGGINS, CF
    TREZISE, AEO
    MACVINISH, LJ
    CUTHBERT, AW
    RATCLIFF, R
    EVANS, MJ
    COLLEDGE, WH
    [J]. NATURE, 1993, 362 (6417) : 250 - 255
  • [6] DEVELOPMENT AND ANALYSIS OF RECOMBINANT ADENOVIRUSES FOR GENE-THERAPY OF CYSTIC-FIBROSIS
    RICH, DP
    COUTURE, LA
    CARDOZA, LM
    GUIGGIO, VM
    ARMENTANO, D
    ESPINO, PC
    HEHIR, K
    WELSH, MJ
    SMITH, AE
    GREGORY, RJ
    [J]. HUMAN GENE THERAPY, 1993, 4 (04) : 461 - 476
  • [7] INVIVO TRANSFER OF THE HUMAN CYSTIC-FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR GENE TO THE AIRWAY EPITHELIUM
    ROSENFELD, MA
    YOSHIMURA, K
    TRAPNELL, BC
    YONEYAMA, K
    ROSENTHAL, ER
    DALEMANS, W
    FUKAYAMA, M
    BARGON, J
    STIER, LE
    STRATFORDPERRICAUDET, L
    PERRICAUDET, M
    GUGGINO, WB
    PAVIRANI, A
    LECOCQ, JP
    CRYSTAL, RG
    [J]. CELL, 1992, 68 (01) : 143 - 155
  • [8] SIMON RH, IN PRESS HUMAN GENE
  • [9] CYSTIC-FIBROSIS - MORE FROM THE MODELERS
    WILSON, JM
    COLLINS, FS
    [J]. NATURE, 1992, 359 (6392) : 195 - 196
  • [10] ADENOVIRUS-MEDIATED GENE-TRANSFER TRANSIENTLY CORRECTS THE CHLORIDE TRANSPORT DEFECT IN NASAL EPITHELIA OF PATIENTS WITH CYSTIC-FIBROSIS
    ZABNER, J
    COUTURE, LA
    GREGORY, RJ
    GRAHAM, SM
    SMITH, AE
    WELSH, MJ
    [J]. CELL, 1993, 75 (02) : 207 - 216