GENE-THERAPY FOR THE HEMOPHILIAS - CURRENT STATUS

被引:5
作者
HOEBEN, RC
机构
[1] Laboratory of Molecular Carcinogenesis and Gene Therapy, Department of Medical Biochemistry, University of Leiden, NL-2333 AL Leiden
关键词
D O I
10.1016/1045-1056(95)90007-1
中图分类号
Q5 [生物化学];
学科分类号
071010 ; 081704 ;
摘要
[No abstract available]
引用
收藏
页码:27 / 29
页数:3
相关论文
共 23 条
[1]   PHENOTYPIC CORRECTION OF FACTOR-IX DEFICIENCY IN SKIN FIBROBLASTS OF HEMOPHILIC DOGS [J].
AXELROD, JH ;
READ, MS ;
BRINKHOUS, KM ;
VERMA, IM .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1990, 87 (13) :5173-5177
[2]  
BRETTLER DB, 1989, BLOOD, V73, P2067
[3]   PURIFIED HUMAN FACTOR-VIII PROCOAGULANT PROTEIN - COMPARATIVE HEMOSTATIC RESPONSE AFTER INFUSIONS INTO HEMOPHILIC AND VONWILLEBRAND DISEASE DOGS [J].
BRINKHOUS, KM ;
SANDBERG, H ;
GARRIS, JB ;
MATTSSON, C ;
PALM, M ;
GRIGGS, T ;
READ, MS .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1985, 82 (24) :8752-8756
[4]   GENE-THERAPY VIA PRIMARY MYOBLASTS - LONG-TERM EXPRESSION OF FACTOR-IX PROTEIN FOLLOWING TRANSPLANTATION INVIVO [J].
DAI, Y ;
ROMAN, M ;
NAVIAUX, RK ;
VERMA, IM .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1992, 89 (22) :10892-10895
[5]   TOWARDS GENE-THERAPY FOR HEMOPHILIA-B USING PRIMARY HUMAN KERATINOCYTES [J].
GERRARD, AJ ;
HUDSON, DL ;
BROWNLEE, GG ;
WATT, FM .
NATURE GENETICS, 1993, 3 (02) :180-183
[6]   NEW TECHNIQUE FOR ASSAY OF INFECTIVITY OF HUMAN ADENOVIRUS 5 DNA [J].
GRAHAM, FL ;
VANDEREB, AJ .
VIROLOGY, 1973, 52 (02) :456-467
[7]   TOWARD GENE-THERAPY FOR HEMOPHILIA-A - LONG-TERM PERSISTENCE OF FACTOR VIII-SECRETING FIBROBLASTS AFTER TRANSPLANTATION INTO IMMUNODEFICIENT MICE [J].
HOEBEN, RC ;
FALLAUX, FJ ;
VANTILBURG, NH ;
CRAMER, SJ ;
VANORMONDT, H ;
BRIET, E ;
VANDEREB, AJ .
HUMAN GENE THERAPY, 1993, 4 (02) :179-186
[8]  
HOEBEN RC, 1992, THROMB HAEMOSTASIS, V67, P341
[9]  
HOEBEN RC, 1990, J BIOL CHEM, V265, P7318
[10]   GENE-THERAPY FOR HUMAN INHERITED DISORDERS - TECHNIQUES AND STATUS [J].
HOEBEN, RC ;
VALERIO, D ;
VANDEREB, AJ ;
VANORMONDT, H .
CRITICAL REVIEWS IN ONCOLOGY HEMATOLOGY, 1992, 13 (01) :33-54