CORRECTION OF NEUTROPHIL CHEMOTAXIS DEFECT IN PATIENTS WITH GAUCHER DISEASE BY LOW-DOSE ENZYME REPLACEMENT THERAPY

被引：26
作者：
ZIMRAN, A
ABRAHAMOV, A
AKER, M
MATZNER, Y
机构：
[1] HADASSAH UNIV HOSP, HEMATOL UNIT, JERUSALEM, ISRAEL
[2] HADASSAH UNIV HOSP, SHAARE ZEDEK MED CTR, GAUCHER CLIN, JERUSALEM, ISRAEL
[3] HADASSAH UNIV HOSP, DEPT PEDIAT, JERUSALEM, ISRAEL
来源：
AMERICAN JOURNAL OF HEMATOLOGY | 1993年 / 43卷 / 01期
关键词：
CEREDASE; INFECTION; GLUCOCEREBROSIDASE;
D O I：
10.1002/ajh.2830430118
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
We have recently described a chemotactic defect in severely afflicted Gaucher disease patients. Two of the patients were treated with low-dose intravenous enzyme replacement (Ceredase). Marked improvement in their hematological status, organomegaly, and growth was observed. In addition, their chemotactic defect and their tendency towards infections were corrected within 1 year of treatment.
引用
收藏
页码：69 / 71
页数：3
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